Intrapleural Administration of a Second-Generation Oxidation Resistant Alpha 1-Antitrypsin Gene Therapy for Alpha 1-Antitrypsin Deficiency

被引：0
|
作者：
Stiles, K. M. [1 ]
Sosulski, M. L. [1 ]
De, B. P. [1 ]
Driscoll, S. R. [1 ]
Kaminsky, S. M. [1 ]
Crystal, R. G. [1 ]
机构：
[1] Weill Cornell Med Coll, New York, NY USA
来源：
AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE | 2020年 / 201卷
关键词：
D O I：
暂无
中图分类号：
R4 [临床医学];
学科分类号：
1002 ; 100602 ;
摘要：
A2284
引用
收藏
页数：1
相关论文
共 50 条
  • [1] Assessment of a Second Generation, Oxidation Resistant Gene Therapy for Alpha 1-Antitrypsin Deficiency
    Sosulski, Meredith L.
    Stiles, Katie M.
    De, Bishnu P.
    Kaminsky, Stephen M.
    Crystal, Ronald G.
    MOLECULAR THERAPY, 2019, 27 (04) : 43 - 43
  • [2] Gene therapy for alpha 1-antitrypsin deficiency with an oxidant-resistant human alpha 1-antitrypsin
    Sosulski, Meredith L.
    Stiles, Katie M.
    Frenk, Esther Z.
    Hart, Fiona M.
    Matsumura, Yuki
    De, Bishnu P.
    Kaminsky, Stephen M.
    Crystal, Ronald G.
    JCI INSIGHT, 2020, 5 (15)
  • [3] Intrapleural "outside-In" Gene Therapy For Alpha 1-Antitrypsin Deficiency
    Chiuchiolo, M. J.
    Kaminsky, S. M.
    Sondhi, D.
    Hackett, N. R.
    Rosenberg, J. B.
    Frenk, E. Z.
    Hwang, Y.
    Van de Graaf, B. G.
    Hutt, J. A.
    Wang, G.
    Benson, J.
    Crystal, R. G.
    AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2014, 189
  • [4] Second Generation Gene Therapy for α1-Antitrypsin Deficiency Using a Genetically Modified α1-Antitrypsin Transgene Resistant to Oxidation
    Sosulski, Meredith L.
    Stiles, Katie M.
    De, Bishnu P.
    Kaminsky, Stephen M.
    Crystal, Ronald G.
    MOLECULAR THERAPY, 2018, 26 (05) : 301 - 301
  • [5] Alpha 1-antitrypsin deficiency
    Faehndrich, Sebastian
    Bals, Robert
    INNERE MEDIZIN, 2024, : 533 - 537
  • [6] Alpha 1-antitrypsin deficiency
    Rooney, C
    Taggert, C
    O'Neill, SJ
    McElvaney, NG
    Coakley, R
    IRISH MEDICAL JOURNAL, 1999, 92 (01) : 227 - 228
  • [7] Alpha 1-antitrypsin deficiency
    Mornex, J. -F.
    REVUE DES MALADIES RESPIRATOIRES, 2022, 39 (08) : 698 - 707
  • [8] alpha 1-antitrypsin deficiency-associated panniculitis: Resolution with intravenous alpha 1-antitrypsin administration and liver transplantation
    ORiordan, K
    Blei, A
    Rao, MS
    Abecassis, M
    TRANSPLANTATION, 1997, 63 (03) : 480 - 482
  • [9] Alpha 1-Antitrypsin Deficiency And Sarcoidosis
    Lonial, K.
    Patel, P.
    Afshar, K.
    AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE, 2014, 189
  • [10] Cluster headache and alpha 1-antitrypsin deficiency
    Summ, O.
    Gregor, N.
    Marziniak, M.
    Gralow, I.
    Husstedt, I. W.
    Evers, S.
    CEPHALALGIA, 2010, 30 (01) : 113 - 117
12345