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AAV vector-mediated muscle directed gene therapy results in long-term enzymatic and functional correction in cardio-vascular system of Fabry mouse
被引:0
|
作者
:
Takahashi, H
论文数:
0
引用数:
0
h-index:
0
机构:
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
Takahashi, H
Seino, Y
论文数:
0
引用数:
0
h-index:
0
机构:
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
Seino, Y
Fukumoto, H
论文数:
0
引用数:
0
h-index:
0
机构:
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
Fukumoto, H
Hirai, Y
论文数:
0
引用数:
0
h-index:
0
机构:
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
Hirai, Y
Shimada, T
论文数:
0
引用数:
0
h-index:
0
机构:
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
Shimada, T
Takano, T
论文数:
0
引用数:
0
h-index:
0
机构:
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
Takano, T
机构
:
[1]
Nippon Med Coll, Dept Internal Med 1, Tokyo 113, Japan
[2]
Nippon Med Coll, Dept Biochem & Mol Biol, Tokyo 113, Japan
来源
:
CIRCULATION
|
2002年
/ 106卷
/ 19期
关键词
:
D O I
:
暂无
中图分类号
:
R5 [内科学];
学科分类号
:
1002 ;
100201 ;
摘要
:
138
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收藏
页码:28 / 28
页数:1
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[42]
AAV2-mediated CLN2 gene transfer to rodent and non-human primate brain results in long-term TPP-I expression compatible with therapy for LINCL
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