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- [2] Long-Term Enzymatic and Phenotypic Correction in the Phenylketonuria Mouse Model by Adeno-Associated Virus Vector-Mediated Gene Transfer Pediatric Research, 2004, 56 : 278 - 284
- [7] Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria Gene Therapy, 2006, 13 : 457 - 462