Efficacy and Safety of Avapritinib in Indolent Systemic Mastocytosis (ISM): Results from the Double Blinded Placebo-Controlled PIONEER Study

被引：0

作者：

Castells, Mariana ^{[1
]}

Gotlib, Jason ^{[2
]}

Elberink, Hanneke Oude ^{[3
]}

Siebenhaar, Frank ^{[4
,5
]}

Hartmann, Karin ^{[6
,7
]}

Broesby-Olsen, Sigurd ^{[8
]}

George, Tracy ^{[9
]}

Panse, Jens ^{[10
]}

Alvarez-Twose, Ivan ^{[11
]}

Radia, Deepti ^{[12
]}

Tashi, Tsewang ^{[13
]}

Livideanu, Cristina Bulai ^{[14
]}

Sabato, Vito ^{[15
,16
]}

Van Daele, Paul ^{[17
]}

Cerquozzi, Sonia ^{[18
,19
]}

Dybedal, Ingunn ^{[20
]}

Reiter, Andreas ^{[21
]}

Pongdee, Thanai ^{[22
]}

Barete, Stephane ^{[23
]}

Schwartz, Lawrence ^{[24
]}

Bose, Prithviraj ^{[25
]}

Triggiani, Massimo ^{[26
]}

Shomali, William ^{[2
]}

Giannetti, Matthew ^{[1
]}

Bidollari, Ilda ^{[27
]}

Lin, Hui-Min ^{[27
]}

Scherber, Robyn ^{[28
]}

Roche, Maria ^{[27
]}

Akin, Cem ^{[29
]}

Maurer, Marcus ^{[4
,5
]}

机构：

[1] Brigham & Womens Hosp, Boston, MA USA

[2] Stanford Univ, Stanford Canc Inst, Sch Med, Stanford, CA USA

[3] Univ Med Ctr Groningen, Groningen, Netherlands

[4] Charit Univ Med Berlin, Berlin, Germany

[5] Fraunhofer Inst Translat Med & Pharmacol ITMP, Frankfurt, Germany

[6] Univ Hosp Basel, Basel, Switzerland

[7] Univ Basel, Basel, Switzerland

[8] Odense Univ Hosp, Odense, Denmark

[9] Univ Utah, ARUP Labs, Sch Med, Salt Lake City, UT USA

[10] Rhein Westfal TH Aachen, Univ Hosp Aachen, Med Fac, Aachen, Germany

[11] Inst Mastocytosis Studies Castilla La Mancha, Toledo, Spain

[12] Guys & St Thomas NHS Fdn Trust, London, England

[13] Univ Utah, Huntsman Canc Inst, Salt Lake City, UT USA

[14] CEREMAST CHU Toulouse, Dept Dermatol, Toulouse, France

[15] Univ Antwerp, Antwerp, Belgium

[16] Antwerp Univ Hosp, Antwerp, Belgium

[17] Erasmus MC, Rotterdam, Netherlands

[18] Univ Calgary, Alberta Hlth Serv, Calgary, AB, Canada

[19] Univ Calgary, Cumming Sch Med, Calgary, AB, Canada

[20] Oslo Univ Hosp, Oslo, Norway

[21] Heidelberg Univ, Univ Hosp Mannheim, Mannheim, Germany

[22] Mayo Clin, Rochester, MN USA

[23] Sorbonne Univ, Pitie Salpetriere Hosp, AP HP, Unit Dermatol Reference Ctr Mastocytosis CEREMAST, Paris, France

[24] Virginia Commonwealth Univ, Richmond, VA USA

[25] Univ Texas MD Anderson Canc Ctr, Houston, TX USA

[26] Univ Salerno, Fisciano, Italy

[27] Blueprint Med Corp, Cambridge, MA USA

[28] UT Hlth San Antonio, MD Anderson Canc Ctr, Blueprint Med Corp, San Antonio, TX USA

[29] Univ Michigan, Ann Arbor, MI USA

来源：

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY | 2023年 / 151卷 / 02期

关键词：

D O I：

暂无

中图分类号：

R392 [医学免疫学];

学科分类号：

100102 ;

摘要：

627

引用

页码：AB204 / AB204

页数：1

共 50 条

[1] Efficacy and Safety of Avapritinib in Indolent Systemic Mastocytosis (ISM): Results From the Double Blinded Placebo-Controlled PIONEER Study
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[5] AVAPRITINIB IMPROVED GASTROINTESTINAL SYMPTOMS IN PATIENTS WITH INDOLENT SYSTEMIC MASTOCYTOSIS: REGISTRATIONAL DOUBLE-BLIND, PLACEBO-CONTROLLED PIONEER STUDY
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