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- [41] Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid PolyneuropathyNEUROLOGY AND THERAPY, 2021, 10 (01) : 375 - 389Coelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Porto, Dept Neurosci, Porto, Portugal Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalAndo, Yukio论文数: 0 引用数: 0 h-index: 0机构: Kumamoto Univ, Grad Sch Med Sci, Dept Neurol, Kumamoto, Japan Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalBenson, Merrill D.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Dept Pathol & Lab Med, Indianapolis, IN 46202 USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Sch Med, Amyloidosis Ctr, Boston, MA 02118 USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalWaddington-Cruz, Marcia论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Univ Hosp, Natl Amyloidosis Referral Ctr CEPARM, Rio De Janeiro, Brazil Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalDyck, Peter J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Dept Neurol, Rochester, MN USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, Div Med, London, England Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalKhella, Sami L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Neurol, Philadelphia, PA 19104 USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalLitchy, William J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Dept Neurol, Rochester, MN USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalMonteiro, Cecilia论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalTai, Li-Jung论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalViney, Nicholas J.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalBuchele, Gustavo论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalBrambatti, Michela论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalJung, Shiangtung W.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalO'Dea, Louis St L.论文数: 0 引用数: 0 h-index: 0机构: Akcea Therapeut, Boston, MA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalTsimikas, Sotirios论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalSchneider, Eugene论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalGeary, Richard S.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalMonia, Brett P.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Ctr Hosp Univ Porto, Dept Neurosci, Porto, PortugalGertz, Morie论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Porto, Dept Neurosci, Porto, Portugal
- [42] Blood Neurofilament Light Chain as a Potential Biomarker for Central and Peripheral Nervous Toxicity in RatsTOXICOLOGICAL SCIENCES, 2022, 185 (01) : 10 - 18Sano, Tomoya论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, Japan Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, JapanMasuda, Yasushi论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Drug Metab & Pharmacokinet Res Labs, Fujisawa, Kanagawa 2518555, Japan Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, JapanYasuno, Hironobu论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, Japan Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, JapanShinozawa, Tadahiro论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, Japan Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, JapanWatanabe, Takeshi论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, Japan Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, JapanKakehi, Masaaki论文数: 0 引用数: 0 h-index: 0机构: Takeda Pharmaceut Co Ltd, Drug Metab & Pharmacokinet Res Labs, Fujisawa, Kanagawa 2518555, Japan Takeda Pharmaceut Co Ltd, Drug Safety Res & Evaluat, 26-1 Muraoka Higashi 2 Chome, Fujisawa, Kanagawa 2518555, Japan
- [43] Neurofilament light chain: A potential biomarker for cerebrovascular disease in children with sickle cell anaemiaBRITISH JOURNAL OF HAEMATOLOGY, 2023, 203 (03) : 460 - 467Green, Nancy S.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USARosano, Caterina论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Dept Epidemiol, Med Ctr, Pittsburgh, PA USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USABangirana, Paul论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Psychiat, Coll Hlth Sci, Kampala, Uganda Global Hlth Uganda, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USA论文数: 引用数: h-index:机构:Munube, Deogratias论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Paediat & Child Hlth, Coll Hlth Sci, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAKasirye, Philip论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Paediat & Child Hlth, Coll Hlth Sci, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAKawooya, Michael论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Radiol, Coll Hlth Sci, Kampala, Uganda Mengo Hosp, Ernest Cook Ultrasound Res & Educ Inst ECUREI, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USALubowa, Samson K.论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Radiol, Coll Hlth Sci, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAMupere, Ezekiel论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Paediat & Child Hlth, Coll Hlth Sci, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAConroy, Andrea论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Dept Pediat, Indianapolis, IN USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAMinja, Frank J.论文数: 0 引用数: 0 h-index: 0机构: Emory Univ, Dept Radiol & Imaging Sci, Sch Med, Atlanta, GA USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USABoehme, Amelia K.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAKang, Min Suk论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAHonig, Lawrence S.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY USA Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USAIdro, Richard论文数: 0 引用数: 0 h-index: 0机构: Makerere Univ, Dept Paediat & Child Hlth, Coll Hlth Sci, Kampala, Uganda Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USA
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- [46] Neurofilament light chain as a potential biomarker for monitoring neurodegeneration in X-linked adrenoleukodystrophyNature Communications, 12Isabelle Weinhofer论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchPaulus Rommer论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchBettina Zierfuss论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchPatrick Altmann论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchMartha Foiani论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchAmanda Heslegrave论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchHenrik Zetterberg论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchAndreas Gleiss论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchPatricia L. Musolino论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchYi Gong论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchSonja Forss-Petter论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchThomas Berger论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchFlorian Eichler论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchPatrick Aubourg论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchWolfgang Köhler论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain ResearchJohannes Berger论文数: 0 引用数: 0 h-index: 0机构: Medical University of Vienna,Department of Pathobiology of the Nervous System, Center for Brain Research
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