Emicizumab Prophylaxis in Infants with Severe Hemophilia A without Factor VIII Inhibitors: Results from the Primary Analysis of the HAVEN 7 Study

被引：2

作者：

Pipe, Steven ^{[1
]}

Collins, Peter ^{[2
]}

Dhalluin, Christophe ^{[3
]}

Kenet, Gili ^{[4
,5
]}

Schmitt, Christophe ^{[3
]}

Buri, Muriel ^{[3
]}

Jimenez-Yuste, Victor ^{[6
]}

Peyvandi, Flora ^{[7
,8
]}

Young, Guy ^{[9
]}

Oldenburg, Johannes ^{[10
]}

Mancuso, Maria Elisa ^{[11
,12
]}

Kavakli, Kaan ^{[13
]}

Kiialainen, Anna ^{[3
]}

Chang, Tiffany ^{[14
]}

Lehle, Michaela ^{[3
]}

Niggli, Markus ^{[3
]}

Fijnvandraat, Karin ^{[15
]}

机构：

[1] Univ Michigan, Ann Arbor, MI 48109 USA

[2] Cardiff Univ, Sch Med, Cardiff, Wales

[3] F Hoffmann La Roche Ltd, Basel, Switzerland

[4] Sheba Med Ctr, Ramat Gan, Israel

[5] Tel Aviv Univ, Tel Aviv, Israel

[6] Univ Autonoma Madrid, La Paz Univ Hosp Idi Paz, Madrid, Spain

[7] Fdn IRCCS Ca Granda Osped Maggiore Policlin, Angelo Bianchi Bonomi Hemophilia & Thrombosis Ctr, Milan, Italy

[8] Univ Milan, Milan, Italy

[9] Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA

[10] Univ Bonn, Bonn, Germany

[11] IRCCS Humanitas Res Hosp, Rozzano, Italy

[12] Humanitas Univ, Rozzano, Italy

[13] Ege Univ, Fac Med, Childrens Hosp, Izmir, Turkiye

[14] Spark Therapeut Inc, San Francisco, CA USA

[15] Univ Amsterdam, Amsterdam, Netherlands

来源：

BLOOD | 2023年 / 142卷

关键词：

D O I：

10.1182/blood-2023-177963

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页数：5

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