.-Globin Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy of α-Thalassemia

被引：0
|
作者：
Segura, Eva [1 ]
Tam, Kevin [1 ]
Fernandez, Beatriz Campo
MacKenzie, Tippi C. [2 ,3 ]
Hollis, Roger
Kohn, Donald B. [1 ]
机构：
[1] UCLA, Los Angeles, CA USA
[2] Univ Calif San Francisco, Eli & Edythe Broad Ctr Regenerat Med, San Francisco, CA USA
[3] Univ Calif San Francisco, San Francisco, CA USA
来源：
BLOOD | 2023年 / 142卷
关键词：
D O I：
10.1182/blood-2023-190619
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
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