.-Globin Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy of α-Thalassemia

被引：0
|
作者：
Segura, Eva [1 ]
Tam, Kevin [1 ]
Fernandez, Beatriz Campo
MacKenzie, Tippi C. [2 ,3 ]
Hollis, Roger
Kohn, Donald B. [1 ]
机构：
[1] UCLA, Los Angeles, CA USA
[2] Univ Calif San Francisco, Eli & Edythe Broad Ctr Regenerat Med, San Francisco, CA USA
[3] Univ Calif San Francisco, San Francisco, CA USA
来源：
BLOOD | 2023年 / 142卷
关键词：
D O I：
10.1182/blood-2023-190619
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
相关论文
共 50 条
  • [1] Alpha Globin Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy of Alpha-Thalassemia
    Gensler, Eva E. R. Segura
    Tam, Kevin
    Campo, Beatriz
    MacKenzie, Tippi C.
    Gregori, Georgia
    Hollis, Roger P.
    Kohn, Donald B.
    MOLECULAR THERAPY, 2023, 31 (04) : 316 - 316
  • [2] .lpha-Globin Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy of Alpha Thalassemia
    Gensler, Eva Segura
    Tam, Kevin
    Fernandez, Beatriz Campo
    Li, Karen
    Mulumba, Carol
    Gutierrez, Andrea
    Hollis, Roger
    MacKenzie, Tippi
    Kohn, Donald
    MOLECULAR THERAPY, 2024, 32 (04) : 554 - 554
  • [3] Lentiviral vectors for gene therapy of α-thalassemia
    Xu, Saijuan
    Liang, Dan
    Cheng, Yan
    Sun, Gongrui
    Zhao, Feiyan
    Yang, Yang
    Zhang, Haokun
    Lai, Yongrong
    Fu, Bin
    Wu, Yuxuan
    SCIENCE CHINA-LIFE SCIENCES, 2025,
  • [4] Development of gene therapy for hematopoietic stem cells using lentiviral vectors
    N-B Woods
    A Ooka
    S Karlsson
    Leukemia, 2002, 16 : 563 - 569
  • [5] Development of gene therapy for hematopoietic stem cells using lentiviral vectors
    Woods, NB
    Ooka, A
    Karlsson, S
    LEUKEMIA, 2002, 16 (04) : 563 - 569
  • [6] In Vivo Application of BaEVRLess-Pseudotyped Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy
    Klatt, Denise
    Liu, Boya
    Mucci, Adele
    Peschers, Marie
    Schiroli, Giulia
    Schambach, Axel
    Harris, Chad
    Pellin, Danilo
    Manis, John P.
    Armant, Myriam
    Scadden, David
    Verhoeyen, Els
    Williams, David A.
    Brendel, Christian
    MOLECULAR THERAPY, 2024, 32 (04) : 147 - 148
  • [7] Lentiviral vectors for the hematopoietic stem cell-based gene therapy of lympho-hematopoietic disorders.
    Trono, D
    Wiznerowicz, M
    BLOOD CELLS MOLECULES AND DISEASES, 2002, 28 (03) : 346 - 346
  • [8] Gene therapy for β-thalassemia using lentiviral vectors encoding either γ-globin or BCL11A/shRNA
    Papanikolaou, E.
    Stamateris, E.
    Georgomanoli, M.
    Wilber, A.
    Sankaran, V. G.
    Hargrove, P. W.
    Kim, Y. S.
    Orkin, S. H.
    Nienhuis, A. W.
    Persons, D. A.
    Anagnou, N. P.
    HUMAN GENE THERAPY, 2010, 21 (10) : 1454 - 1455
  • [9] Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy
    Biffi, Alessandra
    Montini, Eugenio
    Lorioli, Laura
    Cesani, Martina
    Fumagalli, Francesca
    Plati, Tiziana
    Baldoli, Cristina
    Martino, Sabata
    Calabria, Andrea
    Canale, Sabrina
    Benedicenti, Fabrizio
    Vallanti, Giuliana
    Biasco, Luca
    Leo, Simone
    Kabbara, Nabil
    Zanetti, Gianluigi
    Rizzo, William B.
    Mehta, Nalini A. L.
    Cicalese, Maria Pia
    Casiraghi, Miriam
    Boelens, Jaap J.
    Del Carro, Ubaldo
    Dow, David J.
    Schmidt, Manfred
    Assanelli, Andrea
    Neduva, Victor
    Di Serio, Clelia
    Stupka, Elia
    Gardner, Jason
    von Kalle, Christof
    Bordignon, Claudio
    Ciceri, Fabio
    Rovelli, Attilio
    Roncarolo, Maria Grazia
    Aiuti, Alessandro
    Sessa, Maria
    Naldini, Luigi
    SCIENCE, 2013, 341 (6148) : 864 - U58
  • [10] Lentiviral Hematopoietic Stem Cell Gene Therapy in Inherited Metabolic Disorders
    Wagemaker, Gerard
    HUMAN GENE THERAPY, 2014, 25 (10) : 862 - 865
12345