Pilot study for the treatment of cutaneous neurofibromas in neurofibromatosis type 1 patients using topical sirolimus gel

被引：4
|
作者：
Wataya-Kaneda, Mari [1 ,2 ,10 ]
Watanabe, Yoshiyuki [3 ,4 ]
Nakamura, Ayumi [5 ]
Yamamoto, Kouji [6 ]
Okada, Kiyoshi [7 ]
Maeda, Shinichiro [8 ]
Nimura, Keisuke [9 ]
Saga, Kotaro
Katayama, Ichiro [1 ]
机构：
[1] Osaka Univ, Grad Sch Med, Dept Dermatol, Suita, Japan
[2] Osaka Univ, Grad Sch Med, Dept Neurocutaneous Med, Div Hlth Sci, Suita, Japan
[3] Osaka Univ, Grad Sch Med, Dept Radiol, Suita, Japan
[4] Shiga Univ Med Sci, Dept Radiol, Otsu, Japan
[5] Osaka Univ Hosp, Dept Pharm, Suita, Japan
[6] Yokohama City Univ, Sch Med, Dept Biostat, Yokohama, Japan
[7] Osaka Univ, Osaka Univ Hosp, Fac Med, Strateg Global Partnership Cross Innovat Initiat,G, Suita, Japan
[8] Osaka Univ, Grad Sch Pharmaceut Sci, Suita, Japan
[9] Osaka Univ, Grad Sch Med, Dept Genome Biol, Div Gene Therapy Sci, Suita, Japan
[10] Osaka Univ, Grad Sch Med, Dept Dermatol, 2-2 Yamada Oka, Suita, Osaka 5650871, Japan
来源：
JOURNAL OF THE AMERICAN ACADEMY OF DERMATOLOGY | 2023年 / 88卷 / 04期
关键词：
D O I：
10.1016/j.jaad.2022.08.066
中图分类号：
R75 [皮肤病学与性病学];
学科分类号：
100206 ;
摘要：
[No abstract available]
引用
收藏
页码：877 / 880
页数：4
相关论文
共 50 条
  • [11] Lisch nodules in neurofibromatosis type 1: Relationship to age and cutaneous neurofibromas
    Recupero, SM
    Plateroti, R
    Abdolrahimzadeh, S
    DeDominicis, M
    Giustini, S
    Noviello, MR
    Calvieri, S
    ANNALS OF OPHTHALMOLOGY-GLAUCOMA, 1996, 28 (03): : 178 - 183
  • [12] Measuring the Effect of Cutaneous Neurofibromas on Quality of Life in Neurofibromatosis Type 1
    Maguiness, Sheilagh
    Berman, Yemima
    Rubin, Nathan
    Dodds, Melissa
    Plotkin, Scott R.
    Wong, Claire
    Moertel, Christopher
    REiNS Int Collaboration
    NEUROLOGY, 2021, 97 (7S) : S25 - S31
  • [13] Treatment of Cutaneous Neurofibromas in Neurofibromatosis Type 1 With MEK Inhibitor Selumetinib A Nonrandomized Clinical Trial
    Gross, Andrea M.
    Reid, Olivia H.
    Baldwin, Lauren A.
    Cannon, Ashley
    Choo-Wosoba, Hyoyoung
    Steinberg, Seth M.
    Lobbous, Mina
    Wolters, Pamela L.
    Pichard, Dominique C.
    Tibery, Cecilia M.
    Dombi, Eva
    Derdak, Joanne
    Widemann, Brigitte C.
    Korf, Bruce R.
    JAMA DERMATOLOGY, 2025,
  • [14] Cutaneous neurofibromas in Neurofibromatosis type I: a quantitative natural history study
    Cannon, Ashley
    Chen, Mei-Jan
    Li, Peng
    Boyd, Kevin P.
    Theos, Amy
    Redden, David T.
    Korf, Bruce
    ORPHANET JOURNAL OF RARE DISEASES, 2018, 13
  • [15] Effects of imatinib mesylate on cutaneous neurofibromas associated with neurofibromatosis type 1
    Yasuda, Ken-ichi
    Nobeyama, Yoshimasa
    Ishiji, Takaoki
    Ota, Arihito
    Asahina, Akihiko
    CLINICAL CASE REPORTS, 2020, 8 (11): : 2125 - 2128
  • [16] Cutaneous neurofibromas in Neurofibromatosis type I: a quantitative natural history study
    Ashley Cannon
    Mei-Jan Chen
    Peng Li
    Kevin P. Boyd
    Amy Theos
    David T. Redden
    Bruce Korf
    Orphanet Journal of Rare Diseases, 13
  • [17] Measuring the Effect of Cutaneous Neurofibromas on Quality of Life in Neurofibromatosis Type 1
    Maguiness, Sheilagh
    Berman, Yemima
    Rubin, Nathan
    Dodds, Melissa
    Plotkin, Scott R.
    Wong, Claire
    Moertel, Christopher
    NEUROLOGY, 2021, 97 (07) : S25 - S31
  • [18] Sirolimus for progressive neurofibromatosis type 1-associated plexiform neurofibromas: a Neurofibromatosis Clinical Trials Consortium phase II study
    Weiss, Brian
    Widemann, Brigitte C.
    Wolters, Pamela
    Dombi, Eva
    Vinks, Alexander
    Cantor, Alan
    Perentesis, John
    Schorry, Elizabeth
    Ullrich, Nicole
    Gutmann, David H.
    Tonsgard, James
    Viskochil, David
    Korf, Bruce
    Packer, Roger J.
    Fisher, Michael J.
    NEURO-ONCOLOGY, 2015, 17 (04) : 596 - 603
  • [19] Clinical assessment of the use of topical liquid diclofenac following laser microporation of cutaneous neurofibromas in individuals with neurofibromatosis type 1
    Oliveira, Lisa Brauer
    Geller, Mauro
    Cunha, Karin Soares
    Santos, Alessandra
    Bernacchi, Allan
    Rubenstein, Allan E.
    Takirambudde, Sanyu
    Mezitis, Spyros
    Ito Brum, Carolina de Almeida
    Darrigo, Luiz Guilherme, Jr.
    Ribeiro, Marcia Goncalves
    HELIYON, 2021, 7 (03)
  • [20] TOLERABILITY OF THE MTOR INHIBITOR SIROLIMUS IN A PHASE II STUDY FOR NEUROFIBROMATOSIS TYPE 1 (NF1)-ASSOCIATED PLEXIFORM NEUROFIBROMAS: A NEUROFIBROMATOSIS CONSORTIUM STUDY
    Weiss, B.
    Widemann, B. C.
    Cantor, A.
    Perentesis, J.
    Vinks, A.
    Ullrich, N.
    Gutmann, D.
    Korp, B.
    Packer, R.
    Fisher, M. J.
    NEURO-ONCOLOGY, 2010, 12 (06) : II85 - II85
12345