Transduction characteristics of single-stranded and self-complementary AAV2.8 in the porcine retina

被引：0

作者：

Hansen, Silja ^{[1
]}

Lindholm, Anna Bogh ^{[1
]}

Jakobsen, Thomas Stax ^{[1
]}

Aagaard, Lars ^{[1
]}

Bek, Toke ^{[2
]}

Askou, Anne Louise ^{[1
,2
]}

Corydon, Thomas ^{[1
,2
]}

机构：

[1] Aarhus Univ, Biomed, Aarhus, Midtjylland, Denmark

[2] Aarhus Univ Hosp, Dept Ophthalmol, Aarhus, Denmark

来源：

INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2023年 / 64卷 / 08期

关键词：

D O I：

暂无

中图分类号：

R77 [眼科学];

学科分类号：

100212 ;

摘要：

引用

页数：3

共 34 条

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de Vin, Filip
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[22] Efficient Protection of Retina By Tyrosine-Mutated Self-Complementary AAV2 Vector Encoding BDNF in a Rat Retinal Ischemic Injury Model
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[23] Coordination polymers, 14 -: 1D-and 2D-coordination polymers from self-complementary building blocks:: Co-crystallization of (P)- and (M)-single-stranded diastereoisomers
Saalfrank, RW
Maid, H
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[24] Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates
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Ng, Catherine Y. C.
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Davidoff, Andrew M.
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[25] Efficient liver-directed gene therapy for inherited severe hyperbilirubinemia using self-complementary AAV: MMF not just inhibits immune response towards AAV capsid but also impairs liver transduction by ss-AAV but not that by sc-AAV
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[26] Self-complementary adeno-associated virus 2 (AAV)-T cell protein tyrosine phosphatase vector as a helper-virus to improve transduction efficiency of conventional AAV vectors in vitro and in vivo
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Chen, LY
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[27] Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector
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Yamazaki, Yoshiyuki
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Yamamoto, Motoko
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Okada, Takashi
Morita, Akio
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[28] Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector
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[29] In Vitro and In Vivo Efficacy of Single-Strand and Self-Complementary AAV9 Vectors to Treat Isolated Cobalamin B Type Methylmalonic Acidemia
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MOLECULAR THERAPY, 2024, 32 (04) : 91 - 91
[30] Optimized Adeno-Associated Virus (AAV)-Protein Phosphatase-5 Helper Viruses for Efficient Liver Transduction by Single-Stranded AAV Vectors: Therapeutic Expression of Factor IX at Reduced Vector Doses
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Li, Mengxin
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Herzog, Roland W.
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HUMAN GENE THERAPY, 2010, 21 (03) : 271 - 283

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