NGN-401: A Novel Regulated Gene Therapy for Rett Syndrome

被引：0
|
作者：
Jaggumantri, S.
Burstein, S.
Ross, P.
Gadalla, K.
Selfridge, J.
Hector, R.
Thomson, S.
Biezonski, D.
Benito, J.
Albanis, E.
Patroneva, A.
Cobb, S.
机构：
来源：
ANNALS OF NEUROLOGY | 2023年 / 94卷
关键词：
Experimental Therapeutics; Neurodevelopmental Disorders;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
310
引用
收藏
页码：S140 / S140
页数：1
相关论文
共 50 条
  • [21] Development of Regulated Gene Vector to Restore MeCP2 Activity to Treat Rett Syndrome
    Alarifi, Sager
    Twycross, Jamie
    Dixon, James E.
    TISSUE ENGINEERING PART A, 2023, 29 (13-14)
  • [22] CRISPR/Cas9-based gene editing for Rett syndrome therapy
    Croci, S.
    Beligni, G.
    Rossetti, A.
    Edo, A.
    Sorg, T.
    Manara, M.
    Lo Rizzo, C.
    Mencarelli, M. A.
    Canitano, R.
    Sica, M.
    Capitani, K.
    Conticello, S. G.
    Molinaro, F.
    Chiariello, M.
    Chillon, M.
    Ladewig, J.
    Herault, Y.
    Renieri, A.
    Meloni, I.
    HUMAN GENE THERAPY, 2022, 33 (23-24) : A141 - A141
  • [23] Toward gene editing in Rett syndrome
    Meloni, I.
    Croci, S.
    Daga, S.
    Lorenzetti, F. C.
    Papa, F. T.
    Donati, F.
    Lo Rizzo, C.
    Lopergolo, D.
    Doria, M.
    Auricchio, A.
    Conticello, S.
    Renieri, A.
    HUMAN GENE THERAPY, 2018, 29 (12) : A27 - A27
  • [24] Rett Syndrome: between the clinic and the gene
    Clarke, A
    JOURNAL OF MEDICAL GENETICS, 2005, 42 : S36 - S36
  • [25] RETT SYNDROME - A SEARCH FOR GENE SOURCES
    AKESSON, HO
    HAGBERG, B
    WAHLSTROM, J
    ENGERSTROM, IW
    AMERICAN JOURNAL OF MEDICAL GENETICS, 1992, 42 (01): : 104 - 108
  • [26] Rett Syndrome: From the Gene to the Disease
    Matijevic, Tanja
    Knezevic, Jelena
    Slavica, Marko
    Pavelic, Jasminka
    EUROPEAN NEUROLOGY, 2009, 61 (01) : 3 - 10
  • [27] Molecular approaches to the Rett syndrome gene
    Schanen, NC
    JOURNAL OF CHILD NEUROLOGY, 1999, 14 (12) : 806 - 814
  • [28] Two novel mutations in the MECP2 gene in patients with Rett syndrome
    Alashti, Shayan Khalili
    Fallahi, Jafar
    Mohammadi, Sanaz
    Dehghanian, Fatemeh
    Farbood, Zahra
    Masoudi, Marjan
    Poorang, Shiva
    Jokar, Arezoo
    Fardaei, Majid
    GENE, 2020, 732
  • [29] Is riluzole a potential therapy for Rett syndrome?
    Tsai, Shih-Jen
    MEDICAL HYPOTHESES, 2015, 85 (01) : 76 - 78
  • [30] A Novel MECP2 Gene Mutation in a Tunisian Patient with Rett Syndrome
    Fendri-Kriaa, Nourhene
    Abdelkafi, Zaineb
    Ben Rebeh, Imen
    Kamoun, Fatma
    Triki, Chahnez
    Fakhfakh, Faiza
    GENETIC TESTING AND MOLECULAR BIOMARKERS, 2009, 13 (01) : 109 - 113
12345