In Vivo Gene Editing Mitigates Central Nervous System Disease in Lethal Lysosomal Storage Disorder

被引：0
|
作者：
Berkowitz, Cara [1 ]
Dave, Apeksha [1 ]
Luks, Valerie [1 ]
Dumitru, Ana Maria [1 ]
Carpenter, Marco D. [1 ]
Zoltick, Philip W. [1 ]
Peranteau, William H. [1 ]
Riley, John [1 ]
机构：
[1] Childrens Hosp Philadelphia, Philadelphia, PA USA
来源：
JOURNAL OF THE AMERICAN COLLEGE OF SURGEONS | 2023年 / 237卷 / 05期
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R61 [外科手术学];
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页码：S351 / S352
页数：2
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