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- [21] BELUMOSUDIL PHASE 1 DOSE-ESCALATION STUDY IN HEALTHY VOLUNTEERS AND PHASE 2 STUDY IN PATIENTS WITH CGVHD WHO FAILED ≥1 LINE OF SYSTEMIC THERAPY IN CHINABONE MARROW TRANSPLANTATION, 2024, 59 : 308 - 309Wang, Ying论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaWu, Depei论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaZhang, Xiang论文数: 0 引用数: 0 h-index: 0机构: Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaLi, Yuhua论文数: 0 引用数: 0 h-index: 0机构: Southern Med Univ, Zhujiang Hosp, Guangzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaHe, Yanjie论文数: 0 引用数: 0 h-index: 0机构: Southern Med Univ, Zhujiang Hosp, Guangzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaLiu, Qifa论文数: 0 引用数: 0 h-index: 0机构: Nanfang Hosp, Guangzhou, Guangdong, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaXuan, Li论文数: 0 引用数: 0 h-index: 0机构: Nanfang Hosp, Guangzhou, Guangdong, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaLi, Zhenyu论文数: 0 引用数: 0 h-index: 0机构: Xuzhou Med Univ, Affiliated Hosp, Xuzhou, Jiangsu, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaQi, Kunming论文数: 0 引用数: 0 h-index: 0机构: Xuzhou Med Univ, Affiliated Hosp, Xuzhou, Jiangsu, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaSun, Yuqian论文数: 0 引用数: 0 h-index: 0机构: Peking Univ Peoples Hosp, Beijing, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaWang, Shunqing论文数: 0 引用数: 0 h-index: 0机构: Guangzhou First Peoples Hosp, Guangzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaMo, Wenjian论文数: 0 引用数: 0 h-index: 0机构: Guangzhou First Peoples Hosp, Guangzhou, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaGao, Lei论文数: 0 引用数: 0 h-index: 0机构: Army Med Univ, Xinqiao Hosp, Chongqing, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaHua, Ye论文数: 0 引用数: 0 h-index: 0机构: BioNova Pharmaceut Shanghai Ltd, Shanghai, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaWang, Yu论文数: 0 引用数: 0 h-index: 0机构: BioNova Pharmaceut Shanghai Ltd, Shanghai, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaZhang, Ying论文数: 0 引用数: 0 h-index: 0机构: BioNova Pharmaceut Shanghai Ltd, Shanghai, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R ChinaFu, Nico论文数: 0 引用数: 0 h-index: 0机构: Sanofi Med Div, Shanghai, Peoples R China Soochow Univ, Affiliated Hosp 1, Suzhou, Peoples R China
- [22] Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trialLANCET, 2009, 374 (9701): : 1597 - 1605Maguire, Albert M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Childrens Hosp Philadelphia, Dept Hematol, Dept Pediat, Philadelphia, PA 19104 USA Univ Penn, Howard Hughes Med Inst, Philadelphia, PA 19104 USA Univ Iowa, Howard Hughes Med Inst, Iowa City, IA 52242 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAAuricchio, Alberta论文数: 0 引用数: 0 h-index: 0机构: TIGEM, Naples, Italy Univ Naples Federico 2, Dept Pediat, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAWright, J. Fraser论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Sch Med, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAPierce, Eric A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USATesta, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Naples 2, Dept Ophthalmol, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAMingozzi, Federico论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USABennicelli, Jeannette L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAYing, Gui-shuang论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Scheie Eye Inst, Dept Ophthalmol, Ctr Prevent Ophthalmol & Biostat, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USARossi, Settimio论文数: 0 引用数: 0 h-index: 0机构: Univ Naples 2, Dept Ophthalmol, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAFulton, Ann论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Boston, Dept Ophthalmol, Boston, MA USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAMarshall, Kathleen A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USABanfi, Sandra论文数: 0 引用数: 0 h-index: 0机构: TIGEM, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAChung, Daniel C.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAMorgan, Jessica I. W.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAHauck, Bernd论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAZelenaia, Olga论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAZhu, Xiaosong论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USARaffini, Leslie论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Childrens Hosp Philadelphia, Dept Hematol, Dept Pediat, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USACoppieters, Frauke论文数: 0 引用数: 0 h-index: 0机构: Univ Ghent, Ctr Med Genet, B-9000 Ghent, Belgium Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA论文数: 引用数: h-index:机构:Shindler, Kenneth S.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAVolpe, Nicholas J.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Scheie Eye Inst, Dept Ophthalmol, Ctr Prevent Ophthalmol & Biostat, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USASurace, Enrico M.论文数: 0 引用数: 0 h-index: 0机构: TIGEM, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAAcerra, Carmela论文数: 0 引用数: 0 h-index: 0机构: Univ Naples 2, Dept Ophthalmol, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USALyubarsky, Arkady论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USARedmond, T. Michael论文数: 0 引用数: 0 h-index: 0机构: NEI, Lab Retinal Cell & Mol Biol, NIH, Bethesda, MD 20892 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAStone, Edwin论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Howard Hughes Med Inst, Philadelphia, PA 19104 USA Univ Iowa, Howard Hughes Med Inst, Iowa City, IA 52242 USA Univ Iowa, Coll Med, Dept Ophthalmol, Carver Ctr, Iowa City, IA 52242 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USASun, Junwei论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USAMcDonnell, Jennifer Wellman论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA论文数: 引用数: h-index:机构:Simonelli, Francesca论文数: 0 引用数: 0 h-index: 0机构: Univ Naples 2, Dept Ophthalmol, Naples, Italy Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USABennett, Jean论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Abramson Pediat Res Ctr, Philadelphia, PA 19104 USA Univ Penn, Stellar Chance Labs 309C, Scheie Eye Inst, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA
- [23] A phase I/II dose-escalation study of herpes simplex virus type 1 thymidine kinase "suicide" gene therapy for metastatic melanomaHUMAN GENE THERAPY, 1998, 9 (17) : 2585 - 2594Klatzmann, D论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceCherin, P论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceBensimon, G论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceBoyer, O论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceCoutellier, A论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceCharlotte, F论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceBoccaccio, C论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceSalzmann, JL论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, FranceHerson, S论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Lab Biol & Therapeut Pathol Immunitaires, Dept Immunol, F-75651 Paris 13, France
- [24] Phase II and UGT1A1 genotype study of irinotecan dose escalation as salvage therapy for advanced gastric cancerBRITISH JOURNAL OF CANCER, 2012, 106 (10) : 1591 - 1597Jo, J-C论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaLee, J-L论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaRyu, M-H论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaChang, H. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaKim, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Pharm, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaLee, H. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Pharm, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaKim, H-S论文数: 0 引用数: 0 h-index: 0机构: Inje Univ, Coll Med, Dept Pharmacol, Pusan 633165, South Korea Inje Univ, Coll Med, Pharmacogenom Res Ctr, Pusan 633165, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaShin, J-G论文数: 0 引用数: 0 h-index: 0机构: Inje Univ, Coll Med, Dept Pharmacol, Pusan 633165, South Korea Inje Univ, Coll Med, Pharmacogenom Res Ctr, Pusan 633165, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaKim, T-W论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South KoreaKang, Y-K论文数: 0 引用数: 0 h-index: 0机构: Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea Univ Ulsan, Coll Med, Asan Med Ctr, Dept Oncol, Seoul 138736, South Korea
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