Gene Therapy for GM1 Gangliosidosis Mediated by AAV Vector Carrying BBB-Penetrable Enzyme

被引：0
|
作者：
Matsushima, Saki [1 ]
Iizuka, Sayoko [1 ]
Kinoshita, Masafumi [2 ]
Takagi, Haruna [2 ]
Iizuka, Shunsuke [2 ]
Ohtsuki, Kota [2 ]
Imakiire, Atsushi [2 ]
Nagashima, Takashi [3 ]
Okamoto, Shinichiro [4 ,5 ]
Higuchi, Takashi [1 ]
Shimada, Yohta [1 ]
Hioki, Hiroyuki [4 ]
Sonoda, Hiroyuki [2 ]
Watabe, Ayako M. [3 ]
Ohashi, Toya [6 ]
Kobayashi, Hiroshi [1 ]
机构：
[1] Jikei Univ, Div Gene Therapy, Res Ctr Med Sci, Sch Med, Tokyo, Japan
[2] JCR Pharmaceut Co Ltd, Kobe, Hyogo, Japan
[3] Jikei Univ, Inst Clin Med & Res, Res Ctr Med Sci, Sch Med, Chiba, Japan
[4] Juntendo Univ, Dept Neuroanat, Grad Sch Med, Tokyo, Japan
[5] Juntendo Univ, Adv Res Inst Hlth Sci, Tokyo, Japan
[6] Jikei Univ, Sch Nursing, Tokyo, Japan
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1344
引用
收藏
页码：635 / 636
页数：2
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