A severely affected adult type 2 spinal muscular atrophy patient treated with risdiplam

被引：0
|
作者：
Schon, Miguel [1 ]
Domingues, Sara [2 ]
Moreno, Teresa [3 ]
Santos, Miguel Oliveira [1 ,4 ]
机构：
[1] Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Dept Neurosci & Mental Hlth, Ave Prof Egas Moniz, P-1649028 Lisbon, Portugal
[2] Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Dept Phys Med & Rehabil, Lisbon, Portugal
[3] Ctr Hosp Univ Lisboa Norte, Hosp Santa Maria, Pediat Neurol Unit, Lisbon, Portugal
[4] Univ Lisbon, Inst Physiol, Fac Med, Inst Med Mol JLA, Lisbon, Portugal
来源：
NEUROLOGICAL SCIENCES | 2023年 / 44卷 / 04期
关键词：
D O I：
10.1007/s10072-022-06539-1
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：1449 / 1450
页数：2
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