HELIOS-A: IMPACT OF VUTRISIRAN ON QUALITY OF LIFE AND FUNCTIONAL STATUS IN HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS

被引：0
|
作者：
Ajroud-Driss, Senda [1 ]
Berk, John L. [2 ]
Adams, David [3 ,4 ]
Gillmore, Julian [5 ]
Lin, Kon-Ping [6 ]
Kale, Parag [7 ]
Koike, Haruki [8 ]
Aldinc, Emre [9 ]
Chen, Chongshu [9 ]
Vest, John [9 ]
Obici, Laura [10 ]
机构：
[1] Northwestern Univ, Feinberg Sch Med, Dept Med Social Sci, Neurol, Chicago, IL 60611 USA
[2] Boston Med Ctr, Boston, MA USA
[3] Univ Paris Saclay, INSERM, U1195, Le Kremlin Bicetre, France
[4] CHU Bicetre, AP HP, Neurol Dept, Le Kremlin Bicetre, France
[5] UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England
[6] Taipei Vet Gen Hosp, Dept Neurol, Taipei, Taiwan
[7] Baylor Univ, Med Ctr, Dallas, TX USA
[8] Nagoya Univ, Dept Neurol, Grad Sch Med, Nagoya, Aichi, Japan
[9] Alnylam Pharmaceut, Cambridge, MA USA
[10] IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy
来源：
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2023年 / 28卷
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中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
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页码：S40 / S41
页数：2
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