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- [21] Early clinical course after hematopoietic stem cell transplantation in children with juvenile metachromatic leukodystrophyMolecular and Cellular Pediatrics, 7 (1)Judith Beschle论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyMichaela Döring论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyChristiane Kehrer论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyChrista Raabe论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyUte Bayha论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyManuel Strölin论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyJudith Böhringer论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyAndrea Bevot论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyNadja Kaiser论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyBenjamin Bender论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyAlexander Grimm论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyPeter Lang论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyIngo Müller论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologyIngeborg Krägeloh-Mann论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric NeurologySamuel Groeschel论文数: 0 引用数: 0 h-index: 0机构: University Children’s Hospital,Department for Pediatric Neurology
- [22] Long-term Outcome of Allogeneic Hematopoietic Stem Cell Transplantation in Patients With Juvenile Metachromatic Leukodystrophy Compared With Nontransplanted Control PatientsJAMA NEUROLOGY, 2016, 73 (09) : 1133 - 1140Groeschel, Samuel论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyKuehl, Joern-Sven论文数: 0 引用数: 0 h-index: 0机构: Charite Univ Med Berlin, Dept Pediat Oncol, Berlin, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyBley, Annette E.论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyKehrer, Christiane论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyWeschke, Bernhard论文数: 0 引用数: 0 h-index: 0机构: Charite Univ Med Berlin, Dept Neuropediat, Berlin, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyDoering, Michaela论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Dept Pediat Hematol & Oncol, Tubingen, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyBoehringer, Judith论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanySchrum, Johanna论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Hamburg Eppendorf, Dept Pediat Hematol & Oncol, Hamburg, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanySanter, Rene论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyKohlschuetter, Alfried论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Hamburg Eppendorf, Dept Pediat, Hamburg, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyKraegeloh-Mann, Ingeborg论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, GermanyMueller, Ingo论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Dept Pediat Hematol & Oncol, Tubingen, Germany Univ Childrens Hosp Hamburg Eppendorf, Dept Pediat Hematol & Oncol, Hamburg, Germany Univ Childrens Hosp Tubingen, Dept Pediat Neurol & Dev Med, Hoppe Seyler Str 1, D-72076 Tubingen, Germany
- [23] Lentiviral hematopoietic stem cell gene therapy (HSC-GT) for metachromatic leukodystrophy (MLD) provides sustained clinical benefitBONE MARROW TRANSPLANTATION, 2019, 54 : 76 - 77Fumagalli, Francesca论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCalbi, Valeria论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalySessa, Maria论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCugnata, Federica论文数: 0 引用数: 0 h-index: 0机构: Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyRancoita, Paola M. V.论文数: 0 引用数: 0 h-index: 0机构: Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyAcquati, Serena论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyRedaelli, Daniela论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyAttanasio, Vanessa论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyMiglietta, Simona论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyMagni, Sara论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyRecupero, Salvatore论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyFerrua, Francesca论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyBarzaghi, Federica论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCicalese, Maria Pia论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyMigliavacca, Maddalena论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyTucci, Francesca论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyFiori, Rossana论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyFerrari, Maurizio论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalySpiga, Ivana论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalySilvani, Paolo论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyFacchini, Marcella论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyLocatelli, Sara论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyZancan, Stefano论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCiotti, Francesca论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyFraschini, Maddalena论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalySarzana, Marina论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyZambon, Alberto论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCalabria, Andrea论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyMontini, Eugenio论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCanale, Sabrina论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyAntonioli, Gigliola论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyGabaldo, Michela论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyFarinelli, Giada论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyMorena, Francesco论文数: 0 引用数: 0 h-index: 0机构: Univ Perugia, Perugia, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyBaldoli, Cristina论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalySabata, Martino论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyDi Serio, Clelia论文数: 0 引用数: 0 h-index: 0机构: Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyCiceri, Fabio论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalySora, Maria Grazia Natali论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyBernardo, Maria Ester论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyNaldini, Luigi论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyBiffi, Alessandra论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy Univ Padua, Pediat Oncohematol, Padua, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, ItalyAiuti, Alessandro论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SRTIGET, Milan, Italy
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- [27] Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic LeukodystrophySCIENCE, 2013, 341 (6148) : 864 - U58Biffi, Alessandra论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyMontini, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyLorioli, Laura论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyCesani, Martina论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyFumagalli, Francesca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyPlati, Tiziana论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyBaldoli, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyMartino, Sabata论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyCalabria, Andrea论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyCanale, Sabrina论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyBenedicenti, Fabrizio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyVallanti, Giuliana论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyBiasco, Luca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyLeo, Simone论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyKabbara, Nabil论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyZanetti, Gianluigi论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyRizzo, William B.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyMehta, Nalini A. L.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyCicalese, Maria Pia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyCasiraghi, Miriam论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyBoelens, Jaap J.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyDel Carro, Ubaldo论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyDow, David J.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalySchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyAssanelli, Andrea论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyNeduva, Victor论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyDi Serio, Clelia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyStupka, Elia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyGardner, Jason论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italyvon Kalle, Christof论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyBordignon, Claudio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyCiceri, Fabio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyRovelli, Attilio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyRoncarolo, Maria Grazia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyAiuti, Alessandro论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalySessa, Maria论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, ItalyNaldini, Luigi论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy
- [28] Inventory of current practices regarding hematopoietic stem cell transplantation in metachromatic leukodystrophy in Europe and neighboring countriesOrphanet Journal of Rare Diseases, 19Daphne H. Schoenmakers论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalFanny Mochel论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalLaura A. Adang论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalJaap-Jan Boelens论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalValeria Calbi论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalErik A. Eklund论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalSabine W. Grønborg论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalFrancesca Fumagalli论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalSamuel Groeschel论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalCaroline Lindemans论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalCaroline Sevin论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalLudger Schöls论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalDipak Ram论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalAyelet Zerem论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalHolm Graessner论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s HospitalNicole I. Wolf论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC,Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma’s Children’s Hospital
- [29] Inventory of current practices regarding hematopoietic stem cell transplantation in metachromatic leukodystrophy in Europe and neighboring countriesORPHANET JOURNAL OF RARE DISEASES, 2024, 19 (01)Schoenmakers, Daphne H.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, Netherlands Amsterdam Neurosci, Cellular & Mol Mech, Amsterdam, Netherlands Univ Amsterdam, Med Soc, Platform Amsterdam UMC, Amsterdam, Netherlands Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsMochel, Fanny论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, AP HP, Inserm, U1127, Paris, France Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsAdang, Laura A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Child Neurol, Philadelphia, PA USA Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsBoelens, Jaap-Jan论文数: 0 引用数: 0 h-index: 0机构: Mem Sloan Kettering Canc Ctr, Dept Pediat, Stem Cell Transplantat & Cellular Therapies Progra, New York, NY 10065 USA Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsCalbi, Valeria论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR TIGET, Pediat Immunohematol Unit, Via Olgettina 60, I-20132 Milan, Italy IRCCS San Raffaele Sci Inst, Neurol & Neurophysiol Unit, Via Olgettina 60, I-20132 Milan, Italy IRCCS San Raffaele Sci Inst, Pediat Immunohematol Unit, Via Olgettina 60, I-20132 Milan, Italy IRCCS San Raffaele Sci Inst, BMT Program, Via Olgettina 60, I-20132 Milan, Italy Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsEklund, Erik A.论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Skane Univ Hosp & Clin Sci, Sect Pediat Neurol, S-22184 Lund, Sweden Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsGronborg, Sabine W.论文数: 0 引用数: 0 h-index: 0机构: Copenhagen Univ Hosp, Rigshosp, Ctr Inherited Metab Dis, Dept Pediat & Adolescent Med, Copenhagen, Denmark Copenhagen Univ Hosp, Rigshosp, Dept Clin Genet, Copenhagen, Denmark Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsFumagalli, Francesca论文数: 0 引用数: 0 h-index: 0机构: IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR TIGET, Pediat Immunohematol Unit, Via Olgettina 60, I-20132 Milan, Italy IRCCS San Raffaele Sci Inst, Neurol & Neurophysiol Unit, Via Olgettina 60, I-20132 Milan, Italy Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsGroeschel, Samuel论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Paediat Neurol & Dev Med, Tubingen, Germany Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsLindemans, Caroline论文数: 0 引用数: 0 h-index: 0机构: Princess Maxima Ctr Pediat Oncol, Heidelberglaan 25, NL-3584 CS Utrecht, Netherlands Univ Med Ctr Utrecht, Wilhelmina Childrens Hosp, Lundlaan 6, NL-3584 EA Utrecht, Netherlands Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsSevin, Caroline论文数: 0 引用数: 0 h-index: 0机构: Hop Bicetre, Reference Ctr Leukodystrophies, Pediat Neurol Dept, Le Kremlin Bicetre, France Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsSchoels, Ludger论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Dept Neurol, Tubingen, Germany Univ Tubingen, Hertie Inst Clin Brain Res, Tubingen, Germany German Ctr Neurodeenerat Dis DZNE, Tubingen, Germany Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsRam, Dipak论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Dept Paediat Neurol, Manchester, England Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsZerem, Ayelet论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Dana Dwek Childrens Hosp, Pediat Neurol Inst, Sackler Fac Med,Tel Aviv Sourasky Med Ctr, Tel Aviv, Israel Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsGraessner, Holm论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Inst Med Genet & Appl Genom, Ctr Rare Dis, Tubingen, Germany Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, NetherlandsWolf, Nicole I.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, Netherlands Amsterdam Neurosci, Cellular & Mol Mech, Amsterdam, Netherlands Vrije Univ Amsterdam, Emmas Childrens Hosp, Amsterdam Leukodystrophy Ctr, Dept Child Neurol,Amsterdam UMC, Amsterdam, Netherlands
- [30] Long-term outcomes after allogeneic hematopoietic stem cell transplantation for metachromatic leukodystrophy: the largest single-institution cohort reportOrphanet Journal of Rare Diseases, 10Alexander A. Boucher论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and PediatricsWeston Miller论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and PediatricsRyan Shanley论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and PediatricsRichard Ziegler论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and PediatricsTroy Lund论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and PediatricsGerald Raymond论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and PediatricsPaul J. Orchard论文数: 0 引用数: 0 h-index: 0机构: University of Minnesota,Department of Internal Medicine and Pediatrics