共 50 条
- [21] Understanding the Role of LFA-1 in Leukocyte Adhesion Deficiency Type I (LAD I): Moving towards Inflammation?INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2022, 23 (07)Fekadu, Julia论文数: 0 引用数: 0 h-index: 0机构: Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, Germany Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, GermanyModlich, Ute论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Div Vet Med, Res Grp Gene Modificat Stem Cells, D-63225 Langen, Germany Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, GermanyBader, Peter论文数: 0 引用数: 0 h-index: 0机构: Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, Germany Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, GermanyBakhtiar, Shahrzad论文数: 0 引用数: 0 h-index: 0机构: Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, Germany Goethe Univ, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, D-60590 Frankfurt, Germany
- [22] A Phase 1/2 Study of Lentiviral-mediated Ex-vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim ResultsJOURNAL OF CLINICAL IMMUNOLOGY, 2021, 41 (SUPPL 1) : S126 - S126Kohn, Donald论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USARao, Gayatri论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, LAD 1 Program, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAAlmarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USATerrazas, Dayna论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USANicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAFernandes, Augustine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAKuo, Caroline论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USADe Oliveira, Satiro论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAMoore, Theodore论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Pediat Hematol Oncol, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USALaw, Ken论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, CMC, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USABeard, Brian论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, CMC, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USASevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: IB Hosp Infantil Univ Nino Jesus, Madrid, Spain ISCIII, CIBERER, Madrid, Spain Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAMesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: ISCIII, CIBERER, Madrid, Spain Entro Invest Energet Medioambientales & Tecnol CI, Madrid, Spain UAM, IIS FJD, Madrid, Spain Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USABooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St GOS Inst Child Hlth, London, England Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAThrasher, Adrian论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St GOS Inst Child Hlth, London, England Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USABueren, Juan论文数: 0 引用数: 0 h-index: 0机构: ISCIII, CIBERER, Madrid, Spain Entro Invest Energet Medioambientales & Tecnol CI, Madrid, Spain UAM, IIS FJD, Madrid, Spain Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USASchwartz, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA
- [23] A phase 1/2 study of lentiviral-mediated ex-vivo gene therapy for pediatric patients with severe leukocyte adhesion deficiency-I (LAD-I): Interim resultsHUMAN GENE THERAPY, 2021, 32 (19-20) : A5 - A5Booth, C.论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, England UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandKohn, D. B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandSevilla, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Hematol & Hemoterapia, Fdn Invest Biomed HIUNJ, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandRao, G. R.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandAlmarza, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Rocket Pharmaceut Inc, Cranbury, NJ USA Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Hematopoiet Innovat Therapies, Madrid, Spain UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandTerrazas, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandNicoletti, E.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandFernandes, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandKuo, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandDe Oliveira, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandMoore, T. B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandLaw, K. M.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandBeard, B. C.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandChoi, G.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandZeini, M.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandMesa-Nunez, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Hematopoiet Innovat Therapies, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Adv Therapies Unit, Madrid, Spain UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandThrasher, A. J.论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, England UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandBueren, J.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Hematopoiet Innovat Therapies, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Adv Therapies Unit, Madrid, Spain UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, EnglandSchwartz, J.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA UCL Great Ormond St Hosp GOSH, Inst Child Hlth, Infect Immun & Inflammat Dept, London, England
- [24] A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim ResultsBLOOD, 2021, 138Kohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Los Angeles, CA 90024 USABooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA 90024 USASevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus HIUNJ, Hematol & Hemoterapia, Fdn invest Biomed, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA 90024 USARao, Gayathri R.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAAlmarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Ctr Invest Energet Medioambient & Tecnol CIEMAT, Unidad Innovac Biomed, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, ISCIII, Madrid, Spain Unidad Mixta Terapias Avanzadas, Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA 90024 USATerrazas, Dayna论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Los Angeles, CA 90024 USANicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAFernandes, Augustine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAKuo, Caroline论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAOliveira, Satirode论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAMoore, Theodore B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA Univ Calif Los Angeles, Los Angeles, CA 90024 USALaw, Kenneth M.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA 90024 USABeard, Brian C.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAChoi, Grace论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAZeini, Miriam论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA 90024 USAMesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Unidad Innovac Biomed, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, ISCIII, Madrid, Spain Unidad Mixta Terapias Avanzadas, Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA 90024 USAThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA 90024 USABueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Unidad Innovac Biomed, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, ISCIII, Madrid, Spain Unidad Mixta Terapias Avanzadas, Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA 90024 USASchwartz, Jonathan D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA 90024 USA
- [25] A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim ResultsMOLECULAR THERAPY, 2021, 29 (04) : 19 - 20Kohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USARao, Gayatri论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAAlmarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, New York, NJ USA Univ Calif Los Angeles, Los Angeles, CA USATerrazas, Dayna论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USANicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAFernandes, Augustine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USAKuo, Caroline论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USADe Oliviera, Satiro论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USAMoore, Theodore论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USALaw, Ken论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USABeard, Brian论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USASevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: FIB Hosp Infantil Univ Nino Jesus, Pediat Oncol Hematol & Stem Cell Transplant Dept, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USAMesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USABooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St GOS Inst Child Hlth, Infect Immun & Inflammat Dept, London, England Univ Calif Los Angeles, Los Angeles, CA USAThrasher, Adrian论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St GOS Inst Child Hlth, Infect Immun & Inflammat Dept, London, England Univ Calif Los Angeles, Los Angeles, CA USABueren, Juan论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USASchwartz, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USA
- [26] Reduced-intensity conditioning hematopoietic stem cell transplantation in leukocyte adhesion deficiency type I: A single center experienceBONE MARROW TRANSPLANTATION, 2017, 52 : S504 - S504Hamidieh, A. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, Iran Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, IranRostami, T.论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, Iran Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, Iran论文数: 引用数: h-index:机构:Pourpak, Z.论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Immunol Asthma & Allergy Res Inst, Tehran, Iran Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, IranFazlollahi, M. R.论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Immunol Asthma & Allergy Res Inst, Tehran, Iran Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, Iran论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Moin, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Immunol Asthma & Allergy Res Inst, Tehran, Iran Univ Tehran Med Sci, Hematol Oncol & SCT Res Ctr, Tehran, Iran
- [27] Hematopoietic stem cell transplantation for the treatment of leukocyte adhesion deficiency type IIIPEDIATRICS AND NEONATOLOGY, 2017, 58 (06): : 560 - 561Saultier, Paul论文数: 0 引用数: 0 h-index: 0机构: Aix Marseille Univ, INSERM, INRA, NORT, Marseille, France Timone Enfants Hosp, AP HM, Dept Pediat Hematol & Oncol, Marseille, France Aix Marseille Univ, Marseille, France Aix Marseille Univ, INSERM, INRA, NORT, Marseille, FranceAlessi, Marie-Christine论文数: 0 引用数: 0 h-index: 0机构: Aix Marseille Univ, INSERM, INRA, NORT, Marseille, France CHU Timone, AP HM, French Reference Ctr Inherited Platelet Disorders, Marseille, France Aix Marseille Univ, INSERM, INRA, NORT, Marseille, FranceMichel, Gerard论文数: 0 引用数: 0 h-index: 0机构: Aix Marseille Univ, INSERM, INRA, NORT, Marseille, France Timone Enfants Hosp, AP HM, Dept Pediat Hematol & Oncol, Marseille, France Aix Marseille Univ, Marseille, France Aix Marseille Univ, INSERM, INRA, NORT, Marseille, FranceChambost, Herve论文数: 0 引用数: 0 h-index: 0机构: Timone Enfants Hosp, AP HM, Dept Pediat Hematol & Oncol, Marseille, France Aix Marseille Univ, Marseille, France Aix Marseille Univ, INSERM, INRA, NORT, Marseille, France
- [28] Autologous Ex-Vivo Lentiviral Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 StudyMOLECULAR THERAPY, 2023, 31 (04) : 727 - 728Kohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USASevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: HIUNJ CIBERER, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USARao, Gayatri论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USALopez, Maria Chitty论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAAlmarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USATerrazas, Dayna论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USAZubicaray, Josune论文数: 0 引用数: 0 h-index: 0机构: HIUNJ CIBERER, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USAGonzalez-Vicent, Marta论文数: 0 引用数: 0 h-index: 0机构: HIUNJ CIBERER, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USAChetty, Kritika论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA USAO'Toole, Grainne论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA USAXu-Bayford, Jinhua论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA USANicoletti, Eileen论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAFernandez, Augustine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USAKuo, Caroline Y.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USADe Oliveira, Satiro N.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USAMoore, Theodore B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Los Angeles, CA USA Univ Calif Los Angeles, Los Angeles, CA USAChoi, Grace论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAZeini, Miriam论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAMesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USAThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA USABueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER IIS FJD, Madrid, Spain Univ Calif Los Angeles, Los Angeles, CA USASchwartz, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, Cranbury, NJ USA Univ Calif Los Angeles, Los Angeles, CA USABooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Univ Calif Los Angeles, Los Angeles, CA USA
- [29] Sweet syndrome associated with moderate leukocyte adhesion deficiency type I: a case report and review of the literatureFRONTIERS IN IMMUNOLOGY, 2024, 15Saito, Yoshine论文数: 0 引用数: 0 h-index: 0机构: Univ Maryland, Sch Med, Baltimore, MD USA Univ Maryland, Sch Med, Baltimore, MD USAKewalramani, Anupama论文数: 0 引用数: 0 h-index: 0机构: Univ Maryland, Sch Med, Dept Pediat, Div Pulmonol Allergy, Baltimore, MD 21201 USA Univ Maryland, Sch Med, Baltimore, MD USAPeng, Xiao P.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Dept Genet Med, Sch Med, Baltimore, MD USA Univ Maryland, Sch Med, Baltimore, MD USAMagnarelli, Aimee论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Eudowood Div Pediat Allergy Immunol & Rheumatol, Sch Med, Baltimore, MD USA Univ Maryland, Sch Med, Baltimore, MD USALederman, Howard M.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Eudowood Div Pediat Allergy Immunol & Rheumatol, Sch Med, Baltimore, MD USA Univ Maryland, Sch Med, Baltimore, MD USA
- [30] Successful allogeneic stem cell transplantation with a reduced-intensity conditioning in a case of leukocyte adhesion deficiency type IIIHEMATOLOGY TRANSFUSION AND CELL THERAPY, 2024, 46 (03) : 300 - 302Barhoom, Dima论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, Iran Damascus Univ, Childrens Hosp, Pediat Hematopoiet Stem Cell Transplant Ctr, Damascus, Syria Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, IranBehfar, Maryam论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, Iran Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, IranMohseni, Rashin论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, Iran Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, IranHamidieh, Amir Ali论文数: 0 引用数: 0 h-index: 0机构: Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, Iran Univ Tehran Med Sci, Gene Cell & Tissue Res Inst, Pediat Cell & Gene Therapy Res Ctr, Tehran, Iran