Liver-Directed Gene Targeting as a Potential Therapy for Fabry Disease

被引：0
|
作者：
Saxena, Himanshi [1 ]
Biasizzo, Jessica [2 ]
Domenis, Rossana [2 ]
Zentilin, Lorena [1 ]
Dardis, Andrea [3 ]
Muro, Andres F. [1 ]
机构：
[1] Int Ctr Genet Engn & Biotechnol, Trieste, Italy
[2] Univ Hosp Udine, Inst Clin Pathol, Dept Lab Med, Udine, Italy
[3] Univ Hosp Udine, Ctr Rare Dis, Trieste, Italy
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1571
引用
收藏
页码：733 / 733
页数：1
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