Interim non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy for Mucopolysaccharidosis type I Hurler

被引：0
|
作者：
Tucci, F. [1 ]
Filisetti, C. [1 ]
Cossutta, M. [1 ]
Consiglieri, G. [1 ]
Galimberti, L. [1 ]
Catalli, B. [1 ]
Fumagalli, F. [1 ]
Butera, C. [1 ]
Santangelo, R. [1 ]
Colombo, M. [1 ]
Camesasca, C. [1 ]
Darin, S. [1 ]
Facchini, M. [1 ]
Albertazzi, E. [1 ]
Ciceri, F. [1 ]
Naldini, L. [1 ]
Parini, R. [1 ]
Parini, R. [1 ]
Gentner, B. [1 ]
Aiuti, A. [1 ]
Bernardo, M. E. [1 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy, HSR TIGET, Milan, Italy
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P560
引用
收藏
页码：A240 / A240
页数：1
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