Development and Translation of a Novel CRISPR Genome Editing Therapy to Induce Fetal Hemoglobin for Sickle Cell Disease

被引：0

作者：

Katta, Varun ^{[1
]}

Levine, Rachel M. ^{[1
]}

O'Keefe, Kiera ^{[1
]}

Li, Yichao ^{[1
]}

Dempsey, Erin A. ^{[1
]}

Nimmagadda, Nikitha ^{[1
]}

Jang, Yoonjeong ^{[1
]}

Mayberry, Kalin ^{[1
]}

Mayurathan, Thiyagaraj ^{[1
]}

Lazzarotto, Cicera R. ^{[1
]}

Wood, Rachael K. ^{[1
]}

Manquen, Garret ^{[1
]}

Powers, Alicia D. ^{[1
]}

Yao, Yu ^{[1
]}

Uchida, Naoya ^{[2
]}

Fazio, Frank ^{[1
]}

Lockey, Tim ^{[1
]}

Sharma, Akshay ^{[1
]}

Tisdale, John F. ^{[2
]}

Zhou, Sheng ^{[1
]}

Weiss, Mitchell J. ^{[1
]}

Yen, Jonathan S. ^{[1
]}

Tsai, Shengdar Q. ^{[1
]}

机构：

[1] St Jude Childrens Res Hosp, Memphis, TN USA

[2] NIH, Bethesda, MD USA

来源：

MOLECULAR THERAPY | 2024年 / 32卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：2 / 3

页数：2

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