NEUROPATHY IMPAIRMENT AND NUTRITIONAL STATUS WITH EPLONTERSEN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS

被引：0

作者：

Conceicao, Isabel ^{[1
]}

Wixner, Jonas ^{[2
]}

Berk, John ^{[3
]}

Adams, David ^{[4
]}

Polydefkis, Michael ^{[5
]}

Attarian, Shahram ^{[6
]}

Gillmore, Julian ^{[7
]}

Dyck, P. James ^{[8
]}

Coelho, Teresa ^{[9
,10
]}

Chen, Jersey ^{[11
]}

Hardy, Elise ^{[11
]}

Kwoh, Jesse ^{[12
]}

Natman, Jonatan ^{[13
]}

Cruz, Marcia Waddington ^{[14
]}

机构：

[1] Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal

[2] Umea Univ, Umea, Sweden

[3] Boston Univ, Sch Med, Boston, MA USA

[4] Hop Bicetre, Le Kremlin Bicetre, France

[5] Johns Hopkins Univ, Baltimore, MD USA

[6] Ctr Hosp Univ La Timone, Neuromuscular Disorders & ALS Dept, Marseille, France

[7] UCL, Natl Amyloidosis Ctr, London, England

[8] Mayo Clin, Dept Neurol, Rochester, MN USA

[9] Ctr Hosp Univ Santo Antonio, Porto, Portugal

[10] ERN NMD, Paris, France

[11] AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MD USA

[12] Ionis Pharmaceut Inc, Carlsbad, CA USA

[13] AstraZeneca, Global Evidence, BioPharmaceut Med, Gothenburg, Sweden

[14] Univ Fed Rio de Janeiro, Amyloidosis Ctr, CEPARM, Univ Hosp, Rio De Janeiro, Brazil

来源：

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2024年 / 29卷

关键词：

Amyloid; ATTRv; eplontersen; polyneuropathy; transthyretin amyloidosis;

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

P 319

引用

页码：S138 / S138

页数：1

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