Repeated clear benefits of immunotherapy in a patient with Charcot-Marie-Tooth disease carrying a rare point mutation in PMP22

被引:0
|
作者
Kawai, Honami [1 ]
Nishida, Yoichiro [1 ]
Kanda, Takashi [2 ]
Yokota, Takanori [1 ]
机构
[1] Inst Sci Tokyo, Grad Sch Med & Dent Sci, Dept Neurol & Neurol Sci, 1-5-45 Yushima,Bunkyo Ku, Tokyo 1138519, Japan
[2] Yamaguchi Univ, Grad Sch Med, Dept Neurol & Clin Neurosci, Yamaguchi 7558505, Japan
关键词
Charcot-Marie-Tooth disease (CMT); PMP22; Point mutation; Chronic inflammatory demyelinating polyneuropathy (CIDP); Optic neuritis;
D O I
10.1007/s10048-025-00808-9
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
We describe a unique patient who had been diagnosed with inflammatory demyelinating polyneuropathy (CIDP) for 13 years with frequent clear responses to immunotherapies and was finally diagnosed with Charcot-Marie-Tooth disease (CMT) with a rare point mutation in PMP22 (c.320G > A, p.G107D). Some patients diagnosed with young-onset CIDP may have underlying CMT, and extensive genetic testing including point mutations of PMP22 gene is required not to miss the diagnosis.
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页数:4
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