Advancing orphan drug development for rare diseases

被引:0
|
作者
Ko, Jung Min [1 ,2 ]
机构
[1] Seoul Natl Univ, Coll Med, Dept Pediat, Div Clin Genet, 103 Daehak Ro, Seoul 03080, South Korea
[2] Seoul Natl Univ Hosp, Rare Dis Ctr, Seoul, South Korea
关键词
D O I
10.3345/cep.2023.01109
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
引用
收藏
页码:356 / 357
页数:2
相关论文
共 50 条
  • [21] RARE DISEASES AND ORPHAN DRUGS
    DAINA, E
    LANCET, 1994, 343 (8912): : 1560 - 1561
  • [22] Orphan drugs and rare diseases
    Schulze-Bonhage, Andreas
    Stephani, Ulrich
    ZEITSCHRIFT FUR EPILEPTOLOGIE, 2019, 32 (04): : 263 - 263
  • [23] Addressing the needs of Canadians with rare diseases: an evaluation of orphan drug incentives
    Harris, Emily
    JOURNAL OF LAW AND THE BIOSCIENCES, 2018, 5 (03): : 648 - 681
  • [24] Rare and orphan lung diseases
    Cordier, J-F.
    BREATHE, 2005, 2 (02) : 147 - 154
  • [25] Rare diseases and orphan drugs
    Taruscio, Domenica
    Capozzoli, Fiorentino
    Frank, Claudio
    ANNALI DELL ISTITUTO SUPERIORE DI SANITA, 2011, 47 (01): : 83 - 93
  • [26] Rare diseases and "orphan" drugs
    Hillcoat, BL
    MEDICAL JOURNAL OF AUSTRALIA, 1998, 169 (02) : 69 - 70
  • [27] PMDA activities for facilitation of orphan drug development for rare cancers
    Ishiguro, Megumi
    CANCER SCIENCE, 2021, 112 : 161 - 161
  • [28] A comprehensive study of the rare diseases and conditions targeted by orphan drug designations and approvals over the forty years of the Orphan Drug Act
    Lewis J. Fermaglich
    Kathleen L. Miller
    Orphanet Journal of Rare Diseases, 18
  • [29] A comprehensive study of the rare diseases and conditions targeted by orphan drug designations and approvals over the forty years of the Orphan Drug Act
    Fermaglich, Lewis J. J.
    Miller, Kathleen L. L.
    ORPHANET JOURNAL OF RARE DISEASES, 2023, 18 (01)
  • [30] ORPHAN DRUGS FOR RARE DISEASES IN THE EUROPEAN UNION: BRIDGING THE GAP BETWEEN DRUG DEVELOPMENT AND UNMET MEDICAL NEEDS?
    Catala-Lopez, F.
    Peiro, S.
    Genova-Maleras, R.
    Garcia-Altes, A.
    Sanfelix-Gimeno, G.
    Alvarez-Martin, E.
    Morant-Ginestar, C.
    Ridao, M.
    VALUE IN HEALTH, 2011, 14 (07) : A334 - A334