Multicenter retrospective and prospective analysis of emicizumab and FVIII prophylaxis in children with severe hemophilia A

被引:0
|
作者
Hassan, Tamer [1 ]
Lotfy, Gehan [2 ]
Elalfy, Omar [3 ]
Amin, Mervat [4 ]
Elmasry, Zahraa [5 ]
Elhawary, Eslam [6 ]
Darwish, Ahmed [7 ]
Elalfy, Mohsen [8 ]
机构
[1] Zagazig Univ, Dept Pediat, Zagazig, Egypt
[2] Menia Univ, Menia, Egypt
[3] Natl Res Ctr, Complementary Med Dept, Cairo, Egypt
[4] Assiut Univ, Assiut, Egypt
[5] Sohag Univ, Sohag, Egypt
[6] Tanta Univ, Tanta, Egypt
[7] Mansoura Univ, Mansoura, Egypt
[8] Ain Shams Univ, Cairo, Egypt
关键词
Hemophilia A; Factor VIII; Emicizumab;
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
LBA-PP-004
引用
收藏
页码:222 / 223
页数:2
相关论文
共 50 条
  • [41] Prophylaxis treatment in young severe hemophilia A patients: efficacy, FVIII consumption, trough FVIII levels and therapy compliance
    Biondo, F.
    Santoro, C.
    Baldacci, E.
    Leporace, A.
    Mazzucconi, M. G.
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2011, 9 : 928 - 929
  • [42] AOZORA Study: Interim Analysis of Joint Health in Children with Hemophilia A, without FVIII Inhibitors, 3 Years after Initiating Emicizumab
    Shima, Midori
    Takedani, Hideyuki
    Kitsukawa, Kaoru
    Taki, Masashi
    Ishiguro, Akira
    Nagao, Azusa
    Nosaka, Daisuke
    Kyogoku, Yui
    Iwasaki, Keisuke
    Nogami, Keiji
    BLOOD, 2022, 140 : 2742 - 2744
  • [43] Cost-Effectiveness Model of Recombinant FVIII Versus Emicizumab Treatment of Patients With Severe Hemophilia A Without Inhibitors
    Sun, Shawn X.
    Wu, Yanyu
    McDermott, Michael
    van Keep, Marjolijn
    BLOOD, 2019, 134
  • [44] Association of prophylaxis regimen with FVIII and treatment outcomes in Latin America patients with severe hemophilia A
    Perez Bianco, P.
    Berges, A.
    Soto, V.
    Linares, A.
    Krishnan, S.
    Xiong, Y.
    Aguilar, L.
    Gomez, J.
    Arvizu, J.
    Brabata, C.
    HAEMOPHILIA, 2012, 18 : 143 - 143
  • [45] Breakthrough bleeding episodes in pediatric severe hemophilia a patients with and without inhibitors receiving emicizumab prophylaxis: a single-center retrospective review
    Hassan, Eman
    Motwani, Jayashree
    PEDIATRIC HEMATOLOGY AND ONCOLOGY, 2022, 39 (05) : 418 - 426
  • [46] EMICIZUMAB PROPHYLAXIS FOR THE TREATMENT OF INFANTS WITH SEVERE HEMOPHILIA A WITHOUT FACTOR VIII INHIBITORS: PRIMARY ANALYSIS OF THE HAVEN 7 STUDY
    Pipe, Steven W.
    Collins, Peter
    Dhalluin, Christophe
    Kenet, Gili
    Schmitt, Christophe
    Buri, Muriel
    Jimenez-Yuste, Victor
    Peyvandi, Flora
    Young, Guy
    Oldenburg, Johannes
    Mancuso, Maria Elisa
    Kavakli, Kaan
    Kiialainen, Anna
    Niggli, Markus
    Chang, Tiffany
    Lehle, Michaela
    Fijnvandraat, Karin
    AMERICAN JOURNAL OF HEMATOLOGY, 2024, 100 : 99 - 99
  • [47] Emicizumab prophylaxis in people with hemophilia A and inhibitors: a systematic review and meta-analysis
    Prudente, Tiago Paiva
    Camelo, Ricardo Mesquita
    Guimaraes, Rafael Alves
    Roberti, Maria do Rosario Ferraz
    SAO PAULO MEDICAL JOURNAL, 2024, 142 (05):
  • [48] Additional use of Factor VIII to a Patient with Severe Hemophilia a Receiving Emicizumab Prophylaxis from Infancy
    Yagi, Takeshi
    Matsuda, Takehiro
    Inamine, Itsuki
    Higa, Takeshi
    PEDIATRIC BLOOD & CANCER, 2021, 68
  • [49] EMICIZUMAB FOR THE TREATMENT OF INFANTS WITH SEVERE HEMOPHILIA A: INTERIM ANALYSIS OF HAVEN 7
    Pipe, Steven
    Collins, Peter
    Dhalluin, Christophe
    Kenet, Gili
    Schmitt, Christophe
    Buri, Muriel
    Jimenez-Yuste, Victor
    Peyvandi, Flora
    Young, Guy
    Oldenburg, Johannes
    ElisaMancuso, Maria
    Kiialainen, Anna
    Chang, Tiffany
    Lehle, Michaela
    Fijnvandraat, Karin
    PEDIATRIC BLOOD & CANCER, 2023, 70 : S7 - S7
  • [50] Long-term outcomes with emicizumab prophylaxis for hemophilia A with or without FVIII inhibitors from the HAVEN 1-4 studies
    Callaghan, Michael U.
    Negrier, Claude
    Paz-Priel, Ido
    Chang, Tiffany
    Chebon, Sammy
    Lehle, Michaela
    Mahlangu, Johnny
    Young, Guy
    Kruse-Jarres, Rebecca
    Mancuso, Maria Elisa
    Niggli, Markus
    Howard, Monet
    Bienz, Nives Selak
    Shima, Midori
    Jimenez-Yuste, Victor
    Schmitt, Christophe
    Asikanius, Elina
    Levy, Gallia G.
    Pipe, Steven W.
    Oldenburg, Johannes
    BLOOD, 2021, 137 (16) : 2231 - 2242