[1] Georgetown Univ, Lombardi Comprehens Canc Ctr, Med Ctr, Washington, DC USA
[2] Univ Miami, Div Pediat Hematol Oncol, Dept Pediat, Miller Sch Med, Miami, FL USA
[3] Univ Miami, Hemophilia Treatment Ctr, Miami, FL USA
[4] Osped Maggiore Policlin, Fdn IRCCS Ca Granda, Angelo Bianchi Bonomi Hemophilia & Thrombosis Ctr, Milan, Italy
[5] Lund Univ, Dept Translat Med, Malmo, Sweden
[6] Skane Univ Hosp, Dept Hematol Oncol & Radiat Phys, Malmo, Sweden
[7] Bleeding & Clotting Disorders Inst, Peoria, IL USA