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- [3] MORPHOLOGICAL AND BIOCHEMICAL FINDINGS IN A CASE OF MUCOPOLYSACCHARIDOSIS TYPE-III-A (SANFILIPPOS DISEASE TYPE-A) BEITRAGE ZUR PATHOLOGIE, 1975, 154 (03): : 324 - 338
- [4] TYPE III MUCOPOLYSACCHARIDOSIS (SANFILIPPO DISEASE) SEMAINE DES HOPITAUX, 1972, 48 (11): : 248 - &
- [8] Treatment of mucopolysaccharidosis type III (Sanfilippo syndrome) EXPERT OPINION ON ORPHAN DRUGS, 2013, 1 (09): : 717 - 730