[1] Newcastle Univ, Translat & Clin Res Inst, Newcastle Upon Tyne, Tyne & Wear, England
[2] Evidera, London, England
[3] Univ Leuven, Clin Pharmacol & Pharmacotherapy, Leuven, Belgium
[4] Merck & Co Inc, Pharmacoepidemiol Dept, Ctr Observat & Real World Evidence, Rahway, NJ 07065 USA
[5] Univ Utrecht, Univ Med Ctr Utrecht, Julius Ctr Hlth Sci & Primary Care, Utrecht, Netherlands
[6] Muscular Dystrophy UK, London, England
[7] Univ Brighton, Sch Appl Social Sci, Brighton, E Sussex, England
[8] Erasmus Univ, Erasmus Sch Hlth Policy & Management, Rotterdam, Netherlands
[9] Erasmus Univ, Erasmus Choice Modelling Ctr, Rotterdam, Netherlands
[10] Eli Lilly & Co, Global Patient Safety Dept, Indianapolis, IN 46285 USA
[11] Janssen Res & Dev, Titusville, NJ USA