The impact of interrupting enzyme replacement therapy in late-onset Pompe disease

被引：0
|
作者：
Stephan Wenninger
Kristina Gutschmidt
Corinna Wirner
Krisztina Einvag
Federica Montagnese
Benedikt Schoser
机构：
[1] Friedrich-Baur-Institute,Department of Neurology
[2] Ludwig-Maximilians University Munich,undefined
来源：
Journal of Neurology | 2021年 / 268卷
关键词：
Interruption of enzyme replacement therapy; Clinical outcome; Glycogen storage disease type 2; Pompe disease;
D O I：
暂无
中图分类号：
学科分类号：
摘要：
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收藏
页码：2943 / 2950
页数：7
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