Shortened ex vivo transduction for hematopoietic stem cell gene therapy of Hurler disease: impact on hematopoietic reconstitution potential

被引：0
|
作者：
Zonari, E. [1 ]
Bernardo, M. E. [1 ]
Naldini, M. M. [1 ,2 ]
Galasso, I. [1 ,2 ]
Volpin, M. [1 ]
Desantis, G. [1 ]
Montini, E. [1 ]
Aiuti, A. [1 ,2 ]
Gentner, B. [1 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, Italy
来源：
HUMAN GENE THERAPY | 2019年 / 30卷 / 11期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR13
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收藏
页码：A6 / A6
页数：1
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