Clinically Applicable Dosing Regimens of Phosphorodiamidate Morpholino Oligomer Profoundly Improve Behaviour, Activity, and Dystrophic phenotype in mdx mice

被引：0

|

作者：

Malerba, A. ^{[1
]}

Sharp, P. ^{[2
]}

Graham, I. R. ^{[1
]}

Arechavala-Gomeza, V ^{[3
]}

Foster, K. ^{[1
]}

Morgan, J. E. ^{[3
]}

Muntoni, F.

Wells, D. ^{[2
]}

Dickson, G. ^{[1
]}

机构：

[1] Royal Holloway Univ London, Sch Biol Sci, Egham TW20 0EX, Surrey, England

[2] Imperial Coll London, Dept Cellular & Mol Neurosci, Div Neurosci & Mental Hlth, London W12 ONN, England

[3] UCL, Inst Child Hlth, Dubowitz Neuromuscular Ctr, London WC1N 1EH, England

来源：

HUMAN GENE THERAPY | 2010年 / 21卷 / 04期

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D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

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页码：508 / 508

页数：1

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