Development of Nanoparticles to Deliver a CRISPR/Cas9 Therapy for Duchenne Muscular Dystrophy

被引：0
|
作者：
Emami, Michael R. [1 ,2 ,3 ]
Young, Courtney S. [1 ,2 ,3 ]
Ji, Ying [4 ,5 ]
Pyle, April D. [1 ,2 ,6 ]
Meng, Huan [4 ,5 ]
Spencer, Melissa J. [1 ,2 ,3 ]
机构：
[1] Univ Calif Los Angeles, Mol Biol Inst, Los Angeles, CA USA
[2] Univ Calif Los Angeles, Ctr Duchenne Muscular Dystrophy, Los Angeles, CA USA
[3] Univ Calif Los Angeles, Neurol, Los Angeles, CA USA
[4] Univ Calif Los Angeles, Calif Nanosyst Inst, Los Angeles, CA USA
[5] Univ Calif Los Angeles, Div Nanomed, Med, Los Angeles, CA USA
[6] Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
615
引用
收藏
页码：284 / 285
页数：2
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