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- [1] Expanding the AAV Toolbox for Cerebellar Transduction: Identifying and Characterizing Novel Variants in Non-Human Primates and MiceMOLECULAR THERAPY, 2021, 29 (04) : 27 - 27Keiser, Megan S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAChen, Yong Hong论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USARanum, Paul T.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USALiu, Xueyuan论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USACheng, Congsheng论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USALeib, David论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USASmith, Geary论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAMuehlmatt, Amy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USATecedor, Luis论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USADavidson, Beverly L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
- [2] Novel AAV Capsids Demonstrate Strong Retinal Expression in Non-Human Primates After Intravitreal AdministrationINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2019, 60 (09)Kevany, Brian论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USASuh, Susie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USALu, Jennings论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USAPadegimas, Linas论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USAPalczewski, Krzysztof论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USAMiller, Timothy论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA Abeona Therapeut LLC, Prod Dev, Cleveland, OH USA
- [3] Novel AAV Capsids Demonstrate Strong Retinal Expression in Non-Human Primates after Intravitreal AdministrationMOLECULAR THERAPY, 2019, 27 (04) : 113 - 113Kevany, Brian M.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Cleveland, OH USA Abeona Therapeut Inc, Cleveland, OH USASuh, Susie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Ophthalmol, Irvine, CA USA Univ Calif Irvine, Gavin Herbert Eye Inst, Irvine, CA USA Abeona Therapeut Inc, Cleveland, OH USALu, Jennings论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Cleveland, OH USAPadegimas, Linas论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Cleveland, OH USA Abeona Therapeut Inc, Cleveland, OH USAPalczewski, Krzysztof论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Cleveland, OH USAMiller, Timothy J.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Cleveland, OH USA Abeona Therapeut Inc, Cleveland, OH USA
- [4] Novel AAV capsids for delivery to the retina by intravitreal administrationHUMAN GENE THERAPY, 2019, 30 (11) : A21 - A21Kevany, B. M.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Dallas, TX USA Abeona Therapeut Inc, Dallas, TX USASue, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Dallas, TX USALu, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Dallas, TX USAPalczewski, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Abeona Therapeut Inc, Dallas, TX USAPadegimas, L.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Dallas, TX USA Abeona Therapeut Inc, Dallas, TX USAMiller, T. J.论文数: 0 引用数: 0 h-index: 0机构: Abeona Therapeut Inc, Dallas, TX USA Abeona Therapeut Inc, Dallas, TX USA
- [5] NAVIGATE: A Directed Evolution Platform for Engineering Novel Ocular and Muscle AAV Capsids in Non-Human PrimatesMOLECULAR THERAPY, 2024, 32 (04) : 266 - 267Firnberg, Elad论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USATejada, Sigmund K. S.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAYost, Samantha论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAGiles, April R.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAGaynutdinov, Timur论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAChen, Victor论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAFoltz, Steven论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAElliot, Kirk论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAHeithoff, Benjamin P.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USASmith, Jared B.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAGumerson, Jessica论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USALilley, Brendan论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAKarumuthil-Melethil, Subha论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAChoi, Heonhwa论文数: 0 引用数: 0 h-index: 0机构: Rutgers State Univ, Inst Quantitat Biomed, Piscataway, NJ USA REGENXBIO Inc, Rockville, MD USAKaelber, Jason T.论文数: 0 引用数: 0 h-index: 0机构: Rutgers State Univ, Inst Quantitat Biomed, Piscataway, NJ USA REGENXBIO Inc, Rockville, MD USADanos, Olivier F.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USAMercer, Andrew C.论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USALiu, Ye论文数: 0 引用数: 0 h-index: 0机构: REGENXBIO Inc, Rockville, MD USA REGENXBIO Inc, Rockville, MD USA
- [6] Novel Surgical Method for Intravitreal AAV Administration Overcomes Transduction Barriers in Non-Human PrimatesMOLECULAR THERAPY, 2016, 24 : S13 - S14Comander, Jason论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Ocular Genom Inst, Boston, MA USACarvalho, Livia论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USAWassmer, Sarah论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USAXiao, Ru论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USAPlovie, Eva论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USALangsdorf, Aliete论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USALim, Lawrence论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USAEr, Brian Hafl论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Ocular Genom Inst, Boston, MA USAWu, David M.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Ocular Genom Inst, Boston, MA USAEliott, Dean论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Ocular Genom Inst, Boston, MA USAKim, Leo A.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USAVandenberghe, Luk H.论文数: 0 引用数: 0 h-index: 0机构: Ocular Genom Inst, Boston, MA USA Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Dept Ophthalmol, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Ocular Genom Inst, Boston, MA USA
- [7] A Direct Comparison of Five AAV Capsids for Intramuscular Inoculation in Non-Human PrimatesMOLECULAR THERAPY, 2022, 30 (04) : 207 - 207Gardner, Matthew R.论文数: 0 引用数: 0 h-index: 0机构: Emory Univ, Atlanta, GA 30322 USA Emory Univ, Atlanta, GA 30322 USAFarzan, Michael论文数: 0 引用数: 0 h-index: 0机构: Scripps Res Inst, Jupiter, FL USA Emory Univ, Atlanta, GA 30322 USA
- [8] In vivo selection in non-human primates identifies AAV capsids for on-target CSF delivery to spinal cordMOLECULAR THERAPY, 2024, 32 (08) : 2584 - 2603Hanlon, Killian S.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA UCL, London, England Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USACheng, Ming论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAFerrer, Roberto Montoro论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Dept Pediat Neurol, Amsterdam Neurosci, Emma Childrens Hospitaln,Amsterdam UMC,Amsterdam L, Amsterdam, Netherlands Vrije Univ Amsterdam, Ctr Neurogenom & Cognit Res, Dept Complex Trait Genet, Amsterdam Neurosci, Amsterdam, Netherlands Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USARyu, Jae Ryun论文数: 0 引用数: 0 h-index: 0机构: Korea Univ, Dept Anat, Brain Korea 21 Plus Program Biomed Sci, Coll Med, Seoul, South Korea Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USALee, Boram论文数: 0 引用数: 0 h-index: 0机构: Korea Univ, Dept Anat, Brain Korea 21 Plus Program Biomed Sci, Coll Med, Seoul, South Korea Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAde la Cruz, Demitri论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAPatel, Nikita论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAEspinoza, Paula论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USASantoscoy, Miguel C.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAGong, Yi论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USANg, Carrie论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USANguyen, Diane M.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USANammour, Josette论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAClark, Sean W.论文数: 0 引用数: 0 h-index: 0机构: SwanBio Therapeut, Bala Cynwyd 19005, PA USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAHeine, Vivi M.论文数: 0 引用数: 0 h-index: 0机构: Amsterdam UMC, Emma Childrens Hosp, Dept Child & Adolescent Psychiat, Emma Ctr Personalized Med,Amsterdam Neurosci, Amsterdam, Netherlands Vrije Univ Amsterdam, Ctr Neurogen & Cognit Res, Dept Complex Trait Genet, Amsterdam Neurosci, Amsterdam, Netherlands Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USASun, Woong论文数: 0 引用数: 0 h-index: 0机构: Korea Univ, Dept Anat, Brain Korea 21 Plus Program Biomed Sci, Coll Med, Seoul, South Korea Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAKozarsky, Karen论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USAMaguire, Casey A.论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA Harvard Med Sch, Boston, MA 02116 USA SwanBio Therapeut, Bala Cynwyd 19005, PA USA Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02115 USA
- [9] Delayed Inflammatory Response to Intravitreal AAV Gene Transfer in Non-Human PrimatesMOLECULAR THERAPY, 2016, 24 : S35 - S35Wassmer, Sarah论文数: 0 引用数: 0 h-index: 0机构: Grousbeck Gene Therapy Ctr, Boston, MA USA Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAComander, Jason论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USACarvalho, Livia论文数: 0 引用数: 0 h-index: 0机构: Grousbeck Gene Therapy Ctr, Boston, MA USA Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAXiao, Ru论文数: 0 引用数: 0 h-index: 0机构: Grousbeck Gene Therapy Ctr, Boston, MA USA Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAPlovic, Eva论文数: 0 引用数: 0 h-index: 0机构: Grousbeck Gene Therapy Ctr, Boston, MA USA Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USALangsdorf, Aliete论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USALim, Lawrence论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAHafler, Brian论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAWu, David M.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAEliott, Dean论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAKim, Leo A.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USAVandenberghe, Luk H.论文数: 0 引用数: 0 h-index: 0机构: Grousbeck Gene Therapy Ctr, Boston, MA USA Harvard Univ, Sch Med, Dept Ophthalmol, Massachusetts Eye & Ear Infirm, Boston, MA USA Ocular Genom Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA Grousbeck Gene Therapy Ctr, Boston, MA USA
- [10] Novel AAV capsids for intravitreal gene therapy of photoreceptor disordersEMBO MOLECULAR MEDICINE, 2021, 13 (04)Pavlou, Marina论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanySchon, Christian论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyOccelli, Laurence M.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Small Anim Clin Sci, E Lansing, MI 48824 USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyRossi, Axel论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Haematol, Lab Infect Biol & Gene Transfer, Hannover, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyMeumann, Nadja论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Haematol, Lab Infect Biol & Gene Transfer, Hannover, Germany Hannover Med Sch, REBIRTH Res Ctr Translat Regenerat Med, Hannover, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBoyd, Ryan F.论文数: 0 引用数: 0 h-index: 0机构: Charles River Labs, Ophthalmol Serv, Mattawan, MI USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBartoe, Joshua T.论文数: 0 引用数: 0 h-index: 0机构: Charles River Labs, Ophthalmol Serv, Mattawan, MI USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanySiedlecki, Jakob论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyGerhardt, Maximilian J.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBabutzka, Sabrina论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBogedein, Jacqueline论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyWagner, Johanna E.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyPriglinger, Siegfried G.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBiel, Martin论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyPetersen-Jones, Simon M.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Small Anim Clin Sci, E Lansing, MI 48824 USA Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyBuening, Hildegard论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Inst Expt Haematol, Lab Infect Biol & Gene Transfer, Hannover, Germany Hannover Med Sch, REBIRTH Res Ctr Translat Regenerat Med, Hannover, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, GermanyMichalakis, Stylianos论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Pharm, Ctr Integrated Prot Sci Munich, Munich, Germany Ludwig Maximilians Univ Munchen, Dept Ophthalmol, Munich, Germany