Gene replacement therapy for glycogen storage disease type II with recombinant adeno-associated virus serotype 1 (AAV1) vectors

被引:0
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作者
Fraites, TJ [1 ]
Germain, SA [1 ]
Cahill, KS [1 ]
Cloutier, DA [1 ]
Porvasnik, SL [1 ]
Zolotukhin, I [1 ]
Walter, GA [1 ]
Byrne, BJ [1 ]
机构
[1] Univ Florida, Gainesville, FL USA
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中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
637
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页码:127 / 127
页数:1
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