CRISPR/Cas9 Genome Editing to Treat Sickle Cell Disease and B-Thalassemia: Re-Creating Genetic Variants to Upregulate Fetal Hemoglobin Appear Well-Tolerated, Effective and Durable.

被引：0
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作者：
Lin, Michelle I.
Paik, Elizabeth
Mishra, Bibhu
Burkhardt, David
Kernytsky, Andrew
Pettiglio, Michael
Chen, Yi-Shan
Tomkinson, Kaleigh
Woo, Amanda
Cortes, Mauricio
Tan, Siyuan
Borland, Todd D.
Klein, Lawrence
Yen, Angela
Mahajan, Sudipta
Chan, Eric
Eustace, Brenda
Porteus, Matthew
Chakraborty, Tirtha
Cowan, Chad
Novak, Rodger
Lundberg, Ante
机构：
来源：
BLOOD | 2017年 / 130卷
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D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
284
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收藏
页数：2
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    HAEMATOLOGICA, 2017, 102 : 23 - 24
1