Delivery of a Hyper-Accurate Cas9 from Neisseria meningitidis and its Guide All-In-One Adeno-Associated Virus (AAV) Vector for Efficient In Vivo Genome Editing

被引：0

作者：

Ibraheim, Raed R. ^{[1
]}

Song, Chun-Qing ^{[1
]}

Mir, Aamir ^{[1
]}

Amrani, Nadia ^{[1
]}

Xue, Wen ^{[1
,2
]}

Sontheimer, Erik ^{[1
,2
]}

机构：

[1] Univ Massachusetts, Sch Med, RNA Therapeut Inst, Worcester, MA USA

[2] Univ Massachusetts, Sch Med, Program Mol Med, Worcester, MA USA

来源：

MOLECULAR THERAPY | 2018年 / 26卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

794

引用

页码：362 / 362

页数：1

共 13 条

[1] All-in-one adeno-associated virus delivery and genome editing by Neisseria meningitidis Cas9 in vivo
Raed Ibraheim
Chun-Qing Song
Aamir Mir
Nadia Amrani
Wen Xue
Erik J. Sontheimer
Genome Biology, 19
[2] All-in-one adeno-associated virus delivery and genome editing by Neisseria meningitidis Cas9 in vivo
Ibraheim, Raed
Song, Chun-Qing
Mir, Aamir
Amrani, Nadia
Xue, Wen
Sontheimer, Erik J.
GENOME BIOLOGY, 2018, 19
[3] Advances in Genome Editing Using Adeno-Associated Virus Delivery of a Compact, Hyper-Accurate Cas9 with a Dinucleotide PAM
Ibraheim, Raed R.
Edraki, Alireza
Mir, Aamir
Gainetdinov, Ildar
Yoon, Yeonsoo
Song, Chun-Qing
Xue, Wen
Rivera-Perez, Jaime A.
Sontheimer, Erik
MOLECULAR THERAPY, 2019, 27 (04) : 447 - 447
[4] Characterization of Staphylococcus aureus Cas9: a smaller Cas9 for all-in-one adeno-associated virus delivery and paired nickase applications
Friedland, Ari E.
Baral, Reshica
Singhal, Pankhuri
Loveluck, Katherine
Shen, Shen
Sanchez, Minerva
Marco, Eugenio
Gotta, Gregory M.
Maeder, Morgan L.
Kennedy, Edward M.
Kornepati, Anand V. R.
Sousa, Alexander
Collins, McKensie A.
Jayaram, Hari
Cullen, Bryan R.
Bumcrot, David
GENOME BIOLOGY, 2015, 16
[5] Characterization of Staphylococcus aureus Cas9: a smaller Cas9 for all-in-one adeno-associated virus delivery and paired nickase applications
Ari E. Friedland
Reshica Baral
Pankhuri Singhal
Katherine Loveluck
Shen Shen
Minerva Sanchez
Eugenio Marco
Gregory M. Gotta
Morgan L. Maeder
Edward M. Kennedy
Anand V. R. Kornepati
Alexander Sousa
McKensie A. Collins
Hari Jayaram
Bryan R. Cullen
David Bumcrot
Genome Biology, 16
[6] All-in-One Adeno-Associated Virus Delivery for Therapeutic miR-21 Editing by saCas9 In Vivo
Nieland, Lisa
Vrijmoet, Anne B.
Jetten, Isabelle W.
Rufino-Ramos, David
de Reus, Alexandra J. E. M.
Breyne, Koen
Kleinstiver, Benjamin P.
Maguire, Casey A.
Broekman, Marike L. D.
Breakefield, Xandra O.
Abels, Erik R.
MOLECULAR THERAPY, 2024, 32 (04) : 61 - 62
[7] An engineered self-inactivating adeno-associated virus mediated Cas9 delivery system for therapeutic genome editing
Fuentes, C. M.
Chen, A.
Schaffer, D. V.
HUMAN GENE THERAPY, 2019, 30 (11) : A183 - A183
[8] Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo
Ibraheim, Raed
Tai, Phillip W. L.
Mir, Aamir
Javeed, Nida
Wang, Jiaming
Rodriguez, Tomas C.
Namkung, Suk
Nelson, Samantha
Khokhar, Eraj Shafiq
Mintzer, Esther
Maitland, Stacy
Chen, Zexiang
Cao, Yueying
Tsagkaraki, Emmanouela
Wolfe, Scot A.
Wang, Dan
Pai, Athma A.
Xue, Wen
Gao, Guangping
Sontheimer, Erik J.
NATURE COMMUNICATIONS, 2021, 12 (01)
[9] Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo
Raed Ibraheim
Phillip W. L. Tai
Aamir Mir
Nida Javeed
Jiaming Wang
Tomás C. Rodríguez
Suk Namkung
Samantha Nelson
Eraj Shafiq Khokhar
Esther Mintzer
Stacy Maitland
Zexiang Chen
Yueying Cao
Emmanouela Tsagkaraki
Scot A. Wolfe
Dan Wang
Athma A. Pai
Wen Xue
Guangping Gao
Erik J. Sontheimer
Nature Communications, 12
[10] Therapeutic In Vivo Gene Editing Achieved by a Hypercompact CRISPR-Cas12f1 System Delivered with All-in-One Adeno-Associated Virus
Cui, Tongtong
Cai, Bingyu
Tian, Yao
Liu, Xin
Liang, Chen
Gao, Qingqin
Li, Bojin
Ding, Yali
Li, Rongqi
Zhou, Qi
Li, Wei
Teng, Fei
ADVANCED SCIENCE, 2024, 11 (19)

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