New and Evolving Therapies for Cystic Fibrosis Patients

被引：0

作者：

Jabar, Alisha ^{[1
]}

Raissy, Hengameh H. ^{[2
]}

Blake, Kathryn ^{[3
]}

机构：

[1] Univ New Mexico, Dept Pediat, Albuquerque, NM 87131 USA

[2] Univ New Mexico, Hlth Sci Ctr, Dept Pediat, Sch Med, Albuquerque, NM 87131 USA

[3] Nemours Childrens Clin, Biomed Res Dept Floor 1, Jacksonville, FL USA

来源：

PEDIATRIC ALLERGY IMMUNOLOGY AND PULMONOLOGY | 2014年 / 27卷 / 02期

关键词：

MUTATION; ADHERENCE;

D O I：

10.1089/ped.2014.0364

中图分类号：

R392 [医学免疫学];

学科分类号：

100102 ;

摘要：

Cystic fibrosis (CF) is a common autosomal recessive inherited disorder affecting 1 in 2,500 births and similar to 75,000 people in North America, Europe, and Australia. The purpose of this review is to discuss the most recent advances in therapies for CF patients. The CF drug development pipeline provides information regarding the phase of each new therapy and those that are already in use by patients. The ultimate goal of therapy will be to deliver tailored individualized therapies to those who need it the most. This review will focus on new research on CF transmembrane conductance regulator protein modulator agents and the effort of gene therapy.

引用

页码：92 / 94

页数：3

共 50 条

[1] New Therapies in Cystic Fibrosis
Ratjen, Felix
Grasemann, Hartmut
CURRENT PHARMACEUTICAL DESIGN, 2012, 18 (05) : 614 - 627
[2] New therapies for cystic fibrosis
Boyd, AC
PROCEEDINGS OF 25TH EUROPEAN CYSTIC FIBROSIS CONFERENCE, 2002, : 237 - 246
[3] New pulmonary therapies for cystic fibrosis
Ratjen, Felix
CURRENT OPINION IN PULMONARY MEDICINE, 2007, 13 (06) : 541 - 546
[4] Maintenance of nutritional status in patients with cystic fibrosis: new and emerging therapies
Kalnins, Daina
Wilschanski, Michael
DRUG DESIGN DEVELOPMENT AND THERAPY, 2012, 6 : 151 - 161
[5] New approaches to genetic therapies for cystic fibrosis
Boyd, A. Christopher
Guo, Shuling
Huang, Lulu
Kerem, Batsheva
Oren, Yifat S.
Walker, Amy J.
Hart, Stephen L.
JOURNAL OF CYSTIC FIBROSIS, 2020, 19 : S54 - S59
[6] The challenges and promises of new therapies for cystic fibrosis
Pier, Gerald B.
JOURNAL OF EXPERIMENTAL MEDICINE, 2012, 209 (07): : 1235 - 1239
[7] NEW RESPIRATORY THERAPIES IN CYSTIC-FIBROSIS
STABLEFORTH, DE
JOURNAL OF THE ROYAL SOCIETY OF MEDICINE, 1994, 87 : 11 - 16
[8] An update on new and emerging therapies for cystic fibrosis
Hudock, Kristin M.
Clancy, John Paul
EXPERT OPINION ON EMERGING DRUGS, 2017, 22 (04) : 331 - 346
[9] New and emerging targeted therapies for cystic fibrosis
Quon, Bradley S.
Rowe, Steven M.
BMJ-BRITISH MEDICAL JOURNAL, 2016, 352
[10] New and emerging therapies for pulmonary complications of cystic fibrosis
Tonelli, MR
Aitken, ML
DRUGS, 2001, 61 (10) : 1379 - 1385

← 1 2 3 4 5 →