Optimization of Clarin-1 AAV Gene Delivery Vectors to the Mouse Retina

被引:0
|
作者
Stupay, Rachel M. [1 ,2 ]
Zhu, Ping [1 ]
Deng, Wen-tao [1 ]
Chiodo, Vince [1 ]
Boye, Sanford L. [1 ]
Li, Qiuhong [1 ]
Hauswirth, William W. [1 ]
Dinculescu, Astra [1 ]
机构
[1] Univ Florida, Ophthalmol, Gainesville, FL USA
[2] Univ Florida, Interdisciplinary Program Biomed Sci, Genet Concentrat, Gainesville, FL USA
关键词
538 gene transfer/gene therapy; 688; retina; 648; photoreceptors;
D O I
暂无
中图分类号
R77 [眼科学];
学科分类号
100212 ;
摘要
3324
引用
收藏
页数:3
相关论文
共 50 条
  • [1] Localization of Clarin-1 in Photoreceptor Cells and Optimized AAV Gene Delivery of Clarin-1 to the Mouse Retina
    Hauswirth, William W.
    Stupay, Rachel M.
    Zhu, Ping
    Deng, Wen-Tao
    Chiodo, Vince
    Boye, Sanford L.
    Li, Qiuhong
    Dinculescu, Astra
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2015, 56 (07)
  • [2] Clarin-1 expression in the mouse retina
    Geller, SF
    Sankila, EM
    Adato, A
    Flannery, JG
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2003, 44 : U389 - U389
  • [3] AAV-Mediated Clarin-1 Expression in the Mouse Retina: Implications for USH3A Gene Therapy
    Dinculescu, Astra
    Stupay, Rachel M.
    Deng, Wen-Tao
    Dyka, Frank M.
    Min, Seok-Hong
    Boye, Sanford L.
    Chiodo, Vince A.
    Abrahan, Carolina E.
    Zhu, Ping
    Li, Qiuhong
    Strettoi, Enrica
    Novelli, Elena
    Nagel-Wolfrum, Kerstin
    Wolfrum, Uwe
    Smith, W. Clay
    Hauswirth, William W.
    PLOS ONE, 2016, 11 (02):
  • [4] Clarin-1 expression in the inner retina: implications for gene therapy
    Dinculescu, Astra
    Stupay, Rachel M.
    Min, Seok-Hong
    Boye, Sanford L.
    Chiodo, Vince
    Hauswirth, William W.
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2015, 56 (07)
  • [5] Large gene delivery to the retina with AAV vectors: are we there yet?
    Ivana Trapani
    Patrizia Tornabene
    Alberto Auricchio
    Gene Therapy, 2021, 28 : 220 - 222
  • [6] Large gene delivery to the retina with AAV vectors: are we there yet?
    Trapani, Ivana
    Tornabene, Patrizia
    Auricchio, Alberto
    GENE THERAPY, 2021, 28 (05) : 220 - 222
  • [7] Tyrosine Chemically Modified AAV Vectors for Gene Delivery in Retina
    Mevel, Mathieu
    Leray, Aurelien
    Bouzelha, Mohammed
    Gouin, Sebastien
    Demilly, Joanna
    Penaud-Budloo, Magalie
    Adjali, Oumeya
    Ayuso, Eduard
    Deniaud, David
    Cronin, Therese
    MOLECULAR THERAPY, 2021, 29 (04) : 140 - 140
  • [8] Clarin-1 expression in adult mouse and human retina highlights a role of Muller glia in Usher syndrome
    Xu, Lei
    Bolch, Susan N.
    Santiago, Clayton P.
    Dyka, Frank M.
    Akil, Omar
    Lobanova, Ekaterina S.
    Wang, Yuchen
    Martemyanov, Kirill A.
    Hauswirth, William W.
    Smith, W. Clay
    Handa, James T.
    Blackshaw, Seth
    Ash, John D.
    Dinculescu, Astra
    JOURNAL OF PATHOLOGY, 2020, 250 (02): : 195 - 204
  • [9] Clarin-1, Encoded by the Usher Syndrome III Causative Gene, Forms a Membranous Microdomain POSSIBLE ROLE OF CLARIN-1 IN ORGANIZING THE ACTIN CYTOSKELETON
    Tian, Guilian
    Zhou, Yun
    Hajkova, Dagmar
    Miyagi, Masaru
    Dinculescu, Astra
    Hauswirth, William W.
    Palczewski, Krzysztof
    Geng, Ruishuang
    Alagramam, Kumar N.
    Isosomppi, Juha
    Sankila, Eeva-Marja
    Flannery, John G.
    Imanishi, Yoshikazu
    JOURNAL OF BIOLOGICAL CHEMISTRY, 2009, 284 (28) : 18980 - 18993
  • [10] Vectors and Gene Delivery to the Retina
    Planul, Arthur
    Dalkara, Deniz
    ANNUAL REVIEW OF VISION SCIENCE, VOL 3, 2017, 3 : 121 - 140