AAV8-mediated gene therapy of Pompe mice normalizes muscle pathology and corrects motor function deficits

被引：0
|
作者：
Cheng, S. H. [1 ]
Zhao, M. A. [1 ]
Bercury, S. [1 ]
Fidler, J. A. [1 ]
Foley, J. W. [1 ]
Ryan, S. [1 ]
Taksir, T. [1 ]
Shihabuddin, L. S. [1 ]
Ziegler, R. J. [1 ]
机构：
[1] Genzyme Corp, Framingham, MA 01701 USA
来源：
JOURNAL OF INHERITED METABOLIC DISEASE | 2006年 / 29卷
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D O I：
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页码：30 / 30
页数：1
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