Two AAV2/5-mediated RPGR gene augmentation constructs driven by the GRK1 promoter rescue photoreceptor structure and function in a canine model of RPGR X-linked retinitis pigmentosa

被引：0
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作者：
Beltran, William A. [1 ]
Cideciyan, Artur V. [2 ]
Iwabe, Simone [1 ]
Dufour, Valerie [1 ]
Marinho, Felipe Pompeo [1 ]
Ye, Guo-jie [3 ]
Shearman, Mark [3 ]
Chulay, Jeffrey D. [3 ]
Hauswirth, William [4 ]
Jacobson, Samuel G. [2 ]
Aguirre, Gustavo D. [1 ]
机构：
[1] Univ Penn, Sch Vet Med, Dept Clin Studies, Philadelphia, PA 19104 USA
[2] Univ Penn, Scheie Eye Inst, Dept Ophthalmol, Perelman Sch Med, Philadelphia, PA 19104 USA
[3] AGTC, Alachua, FL USA
[4] Univ Florida, Sch Med, Dept Ophthalmol, Gainesville, PA USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2016年 / 57卷 / 12期
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D O I：
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中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
785
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页数：3
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