Rescue of severely affected dystrophin/utrophin deficient mice by morpholino-oligomer mediated exon skipping

被引：0
|
作者：
Goyenvalle, Aurelie [1 ]
Babbs, Arran [1 ]
Powell, Dave [1 ]
Kole, Ryszard [2 ]
Fletcher, Sue [3 ]
Wilton, Steve [3 ]
Davies, Kay [1 ]
机构：
[1] Univ Oxford, Dept Physiol Anat & Genet, MRC, Funct Genom Unit, Oxford OX1 2JD, England
[2] AVI Biopharma, Corvallis, OR USA
[3] Univ Western Australia, Ctr Neuromuscular & Neurol Disorder, Nedlands, WA 6009, Australia
来源：
HUMAN GENE THERAPY | 2009年 / 20卷 / 11期
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中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
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页码：1403 / 1403
页数：1
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