共 50 条
- [5] Gene therapy for RPE65-mediated inherited retinal dystrophy completes phase 3 LANCET, 2017, 390 (10097): : 823 - 824
- [6] An Economic Evaluation of Voretigene Neparvovec for the Treatment of Biallelic RPE65-Mediated Inherited Retinal Dystrophies in the UK Advances in Therapy, 2020, 37 : 1233 - 1247
- [8] Methodological Challenges in the Economic Evaluation of a Gene Therapy for RPE65-Mediated Inherited Retinal Disease: The Value of Vision PharmacoEconomics, 2021, 39 : 383 - 397