Interim Results from a Phase 2, Multicenter, Single-Arm Study to Evaluate the Safety and Efficacy of Deferasirox after Hematopoietic Stem Cell Transplantation in Children with Beta-Thalassemia Major

被引:0
|
作者
Yesilipek, M. Akif [1 ]
Karasu, Gulsun [2 ]
Kaya, Zuhre [3 ]
Kuskonmaz, Baris B. [4 ]
Uygun, Vedat [1 ]
Dag, Ilkiz [5 ]
Birkent, Asli [5 ]
Ertem, Mehmet [6 ]
机构
[1] Bahcesehir Univ, Dept Pediat Hematol, Fac Med, Antalya, Turkey
[2] Bahcesehir Univ, Dept Pediat Hematol, Fac Med, Istanbul, Turkey
[3] Gazi Univ, Dept Pediat Hematol, Fac Med, Ankara, Turkey
[4] Hacettepe Univ, Fac Med, Dept Pediat Hematol, TR-06100 Ankara, Turkey
[5] Gida & Tarim Urunleri San & Tic AS, Novartis Oncol, Novartis Saglik, Istanbul, Turkey
[6] Ankara Univ, Fac Med, Dept Pediat Hematol, TR-06100 Ankara, Turkey
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:4
相关论文
共 50 条
  • [1] A PHASE 2, MULTICENTER, SINGLE-ARM STUDY TO EVALUATE SAFETY AND EFFICACY OF DEFERASIROX AFTER HEMATOPOIETIC STEM CELL TRANSPLANTATION IN CHILDREN WITH BETA-THALASSEMIA MAJOR
    Yesilipek, M. A.
    Karasu, G.
    Kaya, Z.
    Kuskonmaz, B. B.
    Uygun, V.
    Dag, I.
    Ozudogru, O.
    Ertem, M.
    HAEMATOLOGICA, 2016, 101 : 627 - 627
  • [2] A Phase II, Multicenter, Single-Arm Study to Evaluate the Safety and Efficacy of Deferasirox after Hematopoietic Stem Cell Transplantation in Children with β-Thalassemia Major
    Yesilipek, Mehmet Akif
    Karasu, Gulsun
    Kaya, Zuhre
    Kuskonmaz, Baris B.
    Uygun, Vedat
    Dag, Ilkiz
    Ozudogru, Onur
    Ertem, Mehmet
    BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2018, 24 (03) : 613 - 618
  • [3] Safety and efficacy of deferasirox in beta-thalassemia major patients after hematopoietic stem cell transplantation: Baseline data of a phase II, multi-center, single-arm, prospective study
    Yesilipek, M. A.
    Karasu, G.
    Kaya, Z.
    Kuskonmaz, B. B.
    Kansoy, S.
    Kuepesiz, A. O.
    Cetin, M.
    Dag, I.
    Birkent, A.
    Ertem, M.
    BONE MARROW TRANSPLANTATION, 2015, 50 : S497 - S497
  • [4] HEMATOPOIETIC STEM CELL TRANSPLANTATION FOR BETA-THALASSEMIA MAJOR: A SINGLE CENTER EXPERIENCE
    Ertem, M.
    Ileri, T.
    Ince, E. Unal
    Uysal, Z.
    BONE MARROW TRANSPLANTATION, 2014, 49 : S318 - S318
  • [5] DEFERASIROX USE AFTER HEMATOPOIETIC STEM CELL TRANSPLANTATION IN PEDIATRIC PATIENTS WITH β-THALASSEMIA MAJOR: Preliminary Results
    Unal, Sule
    Kuskonmaz, Baris
    Hazirolan, Tuncay
    Eldem, Gonca
    Aytac, Selin
    Cetin, Mualla
    Uckan, Duygu
    Gumruk, Fatma
    PEDIATRIC HEMATOLOGY AND ONCOLOGY, 2010, 27 (06) : 482 - 489
  • [6] Efficacy and Safety of Ruxolitinib in Regularly Transfused Patients with Thalassemia: Results from Single-Arm, Multicenter, Phase 2a Truth Study
    Aydinok, Yesim
    Karakas, Zeynep
    Cassinerio, Elena
    Siritanaratkul, Noppadol
    Kattamis, Antonis
    Maggio, Aurelio
    Hollaender, Norbert
    Mahuzier, Bruyere
    Gadbaw, Brian
    Taher, Ali T.
    BLOOD, 2016, 128 (22)
  • [7] Hematopoietic stem cell transplantation from unrelated donor in children with beta thalassemia major
    Karasu, Gulsun
    Uygun, Vedat
    Daloglu, Hayriye
    Kilic, Suar
    Ozturkmen, Seda
    Dincer, Zeynep
    Hazar, Volkan
    Yesilipek, Akif
    BONE MARROW TRANSPLANTATION, 2018, 53 : 701 - 701
  • [8] Hematopoietic Stem Cell Transplantation From Unrelated Donor in Children with Beta Thalassemia Major
    Karasu, Gulsun
    Uygun, Vedat
    Daloglu, Hayriye
    Kilic, Suar
    Ozturkmen, Seda
    Dincer, Zeynep
    Hazar, Volkan
    Yesilipek, Akif
    BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2018, 24 (03) : S401 - S402
  • [9] Efficacy and Safety of Vedolizumab in Early CD Patients: Interim Results From a Prospective, Single-Arm, Multicenter, Interventional Study
    Liu, Jing
    Li, Yuqin
    Guo, Hong
    Jia, Yan
    Zhang, Hongjie
    Zhu, Liangru
    Gao, Xiang
    Zhang, Heng
    Cao, Qian
    AMERICAN JOURNAL OF GASTROENTEROLOGY, 2024, 119 (10S): : S983 - S984
  • [10] Influence of Pretransplantation Serum Ferritin on Children Beta-Thalassemia Major Undergoing Allogeneic Hematopoietic Stem Cell Transplantation
    Ruan, Yongsheng
    Wu, Xuedong
    Feng, Xiaoqin
    He, Yuelin
    Li, Chunfu
    BLOOD, 2015, 126 (23)