A Novel AAV8-Based Gene Therapy for Duchenne Muscular Dystrophy: Preclinical Studies in the Mdx Mouse

被引：0
|
作者：
Kim, SunJung [1 ]
Barton, Elisabeth R. [2 ]
Foltz, Steven [1 ]
Patel, Hiren [1 ]
Yang, Lin [1 ]
Kim, KwiHye [1 ]
Chan, Gary [1 ]
Qiao, Chunping [1 ]
Liu, Ye [1 ]
Fiscella, Michele [1 ]
Danos, Olivier [1 ]
Buss, Nick [1 ]
机构：
[1] REGENXBIO, Rockville, MD USA
[2] Univ Florida, Gainesville, FL USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1067
引用
收藏
页码：498 / 498
页数：1
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