An Antisense Oligonucleotide for Hereditary Angioedema

被引：6
|
作者：
Longhurst, Hilary J. [1 ,2 ]
Ameratunga, Rohan [1 ,3 ]
机构：
[1] Auckland City Hosp, Dept Immunol, Auckland, New Zealand
[2] Univ Auckland, Dept Med, Auckland, New Zealand
[3] Univ Auckland, Dept Mol Med & Pathol, Auckland, New Zealand
来源：
NEW ENGLAND JOURNAL OF MEDICINE | 2022年 / 386卷 / 11期
关键词：
D O I：
10.1056/NEJMe2201729
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：1083 / 1085
页数：3
相关论文
共 50 条
  • [1] A PHASE 2 STUDY EVALUATING AN ANTISENSE OLIGONUCLEOTIDE TO PREKALLIKREIN IN PATIENTS WITH HEREDITARY ANGIOEDEMA
    Cohn, D.
    Fijen, L.
    Riedl, M.
    Bordone, L.
    Alexander, V.
    Schneider, E.
    Newman, K.
    ANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2021, 127 (05) : S4 - S4
  • [2] Antisense Inhibition of Prekallikrein to Control Hereditary Angioedema
    Cohn, Danny M.
    Viney, Nicholas J.
    Fijen, Laure M.
    Schneider, Eugene
    Alexander, Veronica J.
    Xia, Shuting
    Kaeser, Gwendolyn E.
    Nanavati, Charvi
    Baker, Brenda F.
    Geary, Richard S.
    Levi, Marcel
    Meijers, Joost C. M.
    Stroes, Erik S. G.
    NEW ENGLAND JOURNAL OF MEDICINE, 2020, 383 (13): : 1242 - 1247
  • [3] The Impact on Quality of Life Following Treatment with Plasma Prekallikrein Targeted Oligonucleotide Antisense Therapy in Hereditary Angioedema Patients
    Fijen, Laura
    Bordone, Laura
    Newman, Kenneth
    Alexander, Veronica
    Riedl, Marc
    Schneider, Eugene
    Cohn, Danny
    JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2022, 149 (02) : AB169 - AB169
  • [4] An Open-label Trial With Plasma Prekallikrein Oligonucleotide Antisense Therapy To Control Angioedema Attacks In Hereditary Angioedema Patients With Normal C1-inhibitor
    Cohn, Danny
    Bordone, Laura
    Fijen, Laure
    Alexander, Veronica
    Newman, Kenneth
    Schneider, Eugene
    Riedl, Marc
    Raasch, Jason
    Manning, Michael
    JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2022, 149 (02) : AB165 - AB165
  • [5] Advances of Antisense Oligonucleotide Technology in the Treatment of Hereditary Neurodegenerative Diseases
    Lin, Mengsi
    Hu, Xinyi
    Chang, Shiyi
    Chang, Yan
    Bian, Wenjun
    Hu, Ruikun
    Wang, Jing
    Zhu, Qingwen
    Qiu, Jiaying
    EVIDENCE-BASED COMPLEMENTARY AND ALTERNATIVE MEDICINE, 2021, 2021
  • [6] Antisense oligonucleotide corrects splice abnormality in hereditary myopathy with lactic acidosis
    Sanaker, Petter Schandl
    Toompuu, Marina
    McClorey, Graham
    Bindoff, Laurence A.
    GENE, 2012, 494 (02) : 231 - 236
  • [7] Hereditary Angioedema
    Fernandez Romero, Diego S.
    NEW ENGLAND JOURNAL OF MEDICINE, 2020, 383 (04):
  • [8] HEREDITARY ANGIOEDEMA
    BLOK, PHHM
    BAARSMA, EA
    CLINICAL OTOLARYNGOLOGY, 1982, 7 (05): : 354 - 355
  • [9] Hereditary angioedema
    Gulbahar, Okan
    Gelincik, Asli
    Sin, Aytul
    Gulec, Mustafa
    Yilmaz, Mustafa
    Gokmen, Nihal Mete
    Taskapan, Oktay
    Ardeniz, Omur
    Ozdemir, Oner
    ASTIM ALLERJI IMMUNOLOJI, 2010, 8 (03): : 125 - 138
  • [10] HEREDITARY ANGIOEDEMA
    BRICKMAN, CM
    HOSEA, SW
    INTERNATIONAL JOURNAL OF DERMATOLOGY, 1983, 22 (03) : 141 - 147
12345