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- [1] mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapyNature Communications, 14Lisa Maria Riedmayr论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyKlara Sonnie Hinrichsmeyer论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyStefan Bernhard Thalhammer论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyDavid Manuel Mittas论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyNina Karguth论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyDina Yehia Otify论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacySybille Böhm论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyValentin Johannes Weber论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyMichael David Bartoschek论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyVictoria Splith论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyManuela Brümmer论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyRaphael Ferreira论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyNanda Boon论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyGabriele Maria Wögenstein论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyChristian Grimm论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyJan Wijnholds论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyVerena Mehlfeld论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyStylianos Michalakis论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyStefanie Fenske论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyMartin Biel论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of PharmacyElvir Becirovic论文数: 0 引用数: 0 h-index: 0机构: LMU Munich,Department of Pharmacy
- [2] mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapyNATURE COMMUNICATIONS, 2023, 14 (01)Riedmayr, Lisa Maria论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyHinrichsmeyer, Klara Sonnie论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyThalhammer, Stefan Bernhard论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyMittas, David Manuel论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyKarguth, Nina论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyOtify, Dina Yehia论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyBoehm, Sybille论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, D-82152 Planegg, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyWeber, Valentin Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Univ Hosp Zurich, Dept Ophthalmol, Lab Retinal Gene Therapy, CH-8952 Schlieren, Switzerland Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyBartoschek, Michael David论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, D-82152 Planegg, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanySplith, Victoria论文数: 0 引用数: 0 h-index: 0机构: ViGeneron GmbH, D-82152 Planegg, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyBruemmer, Manuela论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyFerreira, Raphael论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Genet Dept, Boston, MA 02115 USA Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyBoon, Nanda论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Dept Ophthalmol, Med Ctr LUMC, NL-2333 ZA Leiden, Netherlands Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyWoegenstein, Gabriele Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Univ Hosp Zurich, Dept Ophthalmol, Lab Retinal Cell Biol, CH-8952 Schlieren, Switzerland Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyGrimm, Christian论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Univ Hosp Zurich, Dept Ophthalmol, Lab Retinal Cell Biol, CH-8952 Schlieren, Switzerland Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyWijnholds, Jan论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Dept Ophthalmol, Med Ctr LUMC, NL-2333 ZA Leiden, Netherlands Inst Royal Netherlands Acad Arts & Sci KNAW, Netherlands Inst Neurosci, NL-1105 BA Amsterdam, Netherlands Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyMehlfeld, Verena论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyMichalakis, Stylianos论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Univ Hosp, Dept Ophthalmol, D-80336 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyFenske, Stefanie论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany German Ctr Cardiovasc Res DZHK, Partner Site Munich Heart Alliance, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyBiel, Martin论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, GermanyBecirovic, Elvir论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Univ Hosp Zurich, Dept Ophthalmol, Lab Retinal Gene Therapy, CH-8952 Schlieren, Switzerland Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, D-81377 Munich, Germany
- [3] Efficient therapeutic genome editing in the horseTRANSGENIC RESEARCH, 2018, 27 (05) : 482 - 482Pinzon, C.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USASnyder, M.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USALazzarotto, C.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Univ Fortaleza, Fortaleza, Ceara, Brazil Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USASkenandore, C.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USAHernandez, C.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Large Anim Clin Sci, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USAMoreno, N.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USAHorn, D.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USAGolding, M.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USAVarner, D. D.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Large Anim Clin Sci, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USALong, C.论文数: 0 引用数: 0 h-index: 0机构: Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA Texas A&M Univ, Dept Physiol & Pharmacol, College Stn, TX USA
- [4] Genome Editing Techniques and Their Therapeutic ApplicationsCLINICAL PHARMACOLOGY & THERAPEUTICS, 2017, 101 (01) : 42 - 51Calos, M. P.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Genet, Stanford, CA 94305 USA Stanford Univ, Sch Med, Dept Genet, Stanford, CA 94305 USA
- [5] Cross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editingNature Communications, 13Trevor J. Gonzalez论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyKatherine E. Simon论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyLeo O. Blondel论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyMarco M. Fanous论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyAngela L. Roger论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyMaribel Santiago Maysonet论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyGarth W. Devlin论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyTimothy J. Smith论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyDaniel K. Oh论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyL. Patrick Havlik论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyRuth M. Castellanos Rivera论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyJorge A. Piedrahita论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyMai K. ElMallah论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyCharles A. Gersbach论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and MicrobiologyAravind Asokan论文数: 0 引用数: 0 h-index: 0机构: Duke University School of Medicine,Department of Molecular Genetics and Microbiology
- [6] Cross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editingNATURE COMMUNICATIONS, 2022, 13 (01)Gonzalez, Trevor J.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USASimon, Katherine E.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA North Carolina State Univ, Coll Vet Med, Raleigh, NC USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USABlondel, Leo O.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAFanous, Marco M.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USARoger, Angela L.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Pediat, Sch Med, Durham, NC 27706 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAMaysonet, Maribel Santiago论文数: 0 引用数: 0 h-index: 0机构: StrideBio Inc, Durham, NC USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USADevlin, Garth W.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USASmith, Timothy J.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAOh, Daniel K.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAHavlik, L. Patrick论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USACastellanos Rivera, Ruth M.论文数: 0 引用数: 0 h-index: 0机构: StrideBio Inc, Durham, NC USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAPiedrahita, Jorge A.论文数: 0 引用数: 0 h-index: 0机构: North Carolina State Univ, Coll Vet Med, Raleigh, NC USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAElMallah, Mai K.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Pediat, Sch Med, Durham, NC 27706 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAGersbach, Charles A.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Duke Regenerat Ctr, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USAAsokan, Aravind论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USA Duke Univ, Sch Med, Dept Surg, Durham, NC 27708 USA Duke Univ, Sch Med, Duke Regenerat Ctr, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27706 USA Duke Univ, Sch Med, Dept Mol Genet & Microbiol, Durham, NC 27708 USA
- [7] Genome editing technology and medical applicationsScience China(Life Sciences), 2024, 67 (12) : 2537 - 2539Liren Wang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Frontiers Science Center of Genome Editing and Cell Therapy, Shanghai Key Laboratory of Regulatory Biology, Institute of Biomedical Sciences and School of Life Sciences, East China Normal University Shanghai Frontiers Science Center of Genome Editing and Cell Therapy, Shanghai Key Laboratory of Regulatory Biology, Institute of Biomedical Sciences and School of Life Sciences, East China Normal UniversityBin Zhou论文数: 0 引用数: 0 h-index: 0机构: State Key Laboratory of Cell Biology, CAS Center for Excellence in Molecular Cell Science, Shanghai Institute of Biochemistry and Cell Biology, Chinese Academy of Sciences, University of Chinese Academy of Shanghai Frontiers Science Center of Genome Editing and Cell Therapy, Shanghai Key Laboratory of Regulatory Biology, Institute of Biomedical Sciences and School of Life Sciences, East China Normal UniversityDali Li论文数: 0 引用数: 0 h-index: 0机构: Shanghai Frontiers Science Center of Genome Editing and Cell Therapy, Shanghai Key Laboratory of Regulatory Biology, Institute of Biomedical Sciences and School of Life Sciences, East China Normal University Shanghai Frontiers Science Center of Genome Editing and Cell Therapy, Shanghai Key Laboratory of Regulatory Biology, Institute of Biomedical Sciences and School of Life Sciences, East China Normal University
- [8] Genome editing technology and medical applicationsSCIENCE CHINA-LIFE SCIENCES, 2024, 67 (12) : 2537 - 2539Wang, Liren论文数: 0 引用数: 0 h-index: 0机构: East China Normal Univ, Inst Biomed Sci, Shanghai Frontiers Sci Ctr Genome Editing & Cell T, Sch Life Sci,Shanghai Key Lab Regulatory Biol, Shanghai 200241, Peoples R China East China Normal Univ, Inst Biomed Sci, Shanghai Frontiers Sci Ctr Genome Editing & Cell T, Sch Life Sci,Shanghai Key Lab Regulatory Biol, Shanghai 200241, Peoples R ChinaZhou, Bin论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, CAS Ctr Excellence Mol Cell Sci, Shanghai Inst Biochem & Cell Biol, State Key Lab Cell Biol,Chinese Acad Sci, Shanghai 200031, Peoples R China East China Normal Univ, Inst Biomed Sci, Shanghai Frontiers Sci Ctr Genome Editing & Cell T, Sch Life Sci,Shanghai Key Lab Regulatory Biol, Shanghai 200241, Peoples R ChinaLi, Dali论文数: 0 引用数: 0 h-index: 0机构: East China Normal Univ, Inst Biomed Sci, Shanghai Frontiers Sci Ctr Genome Editing & Cell T, Sch Life Sci,Shanghai Key Lab Regulatory Biol, Shanghai 200241, Peoples R China East China Normal Univ, Inst Biomed Sci, Shanghai Frontiers Sci Ctr Genome Editing & Cell T, Sch Life Sci,Shanghai Key Lab Regulatory Biol, Shanghai 200241, Peoples R China
- [9] Emerging therapeutic applications of CRISPR genome editingEMERGING TOPICS IN LIFE SCIENCES, 2019, 3 (03) : 257 - 260Qasim, Waseem论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, 30 Guilford St, London WC1N 1EH, England UCL, Great Ormond St Inst Child Hlth, 30 Guilford St, London WC1N 1EH, England
- [10] Synthetic sgRNA enables highly efficient CRISPR editing of primary cells for therapeutic applicationsHUMAN GENE THERAPY, 2017, 28 (12) : A66 - A66Holden, K.论文数: 0 引用数: 0 h-index: 0机构: Synthego, Redwood City, CA USA Synthego, Redwood City, CA USAMaures, T.论文数: 0 引用数: 0 h-index: 0机构: Synthego, Redwood City, CA USA Synthego, Redwood City, CA USAWalker, J.论文数: 0 引用数: 0 h-index: 0机构: Synthego, Redwood City, CA USA Synthego, Redwood City, CA USABak, R.论文数: 0 引用数: 0 h-index: 0机构: Aarhus Univ, Aarhus, Denmark Synthego, Redwood City, CA USAHouse, I.论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Munich, Germany Synthego, Redwood City, CA USAWiebking, V.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Stanford, CA 94305 USA Synthego, Redwood City, CA USA