共 50 条
- [1] Neural stem cells for disease modeling of Wolman disease and evaluation of therapeuticsORPHANET JOURNAL OF RARE DISEASES, 2017, 12Aguisanda, Francis论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA Stanford Univ, Sch Med, Inst Stem Cell Biol & Regenerat Med, Stanford, CA 94305 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USAYeh, Charles D.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USAChen, Catherine Z.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USALi, Rong论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USABeers, Jeanette论文数: 0 引用数: 0 h-index: 0机构: NHLBI, iPSC Core, NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USAZou, Jizhong论文数: 0 引用数: 0 h-index: 0机构: NHLBI, iPSC Core, NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USAThorne, Natasha论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA US FDA, Ctr Devices & Radiol Hlth, Silver Spring, MD 20903 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USAZheng, Wei论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Adv Translat Sci, Bldg 10, Bethesda, MD 20892 USA
- [2] Neural stem cells for disease modeling of Wolman disease and evaluation of therapeuticsOrphanet Journal of Rare Diseases, 12Francis Aguisanda论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineCharles D. Yeh论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineCatherine Z. Chen论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineRong Li论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineJeanette Beers论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineJizhong Zou论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineNatasha Thorne论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative MedicineWei Zheng论文数: 0 引用数: 0 h-index: 0机构: National Center for Advancing Translational Sciences,Present Address: Institute for Stem Cell Biology and Regenerative Medicine
- [3] Editorial: Exploring the role of exosomes in disease progression and therapeutics in neurodegenerationFRONTIERS IN AGING NEUROSCIENCE, 2023, 15Jan, Arif Tasleem论文数: 0 引用数: 0 h-index: 0机构: Baba Ghulam Shah Badshah Univ, Sch Biosci & Biotechnol, Gene Express Lab, Rajouri, India Baba Ghulam Shah Badshah Univ, Sch Biosci & Biotechnol, Gene Express Lab, Rajouri, IndiaRahman, Safikur论文数: 0 引用数: 0 h-index: 0机构: Babasaheb Bhimrao Ambedkar Bihar Univ, Munshi Singh Coll, Dept Bot, Muzaffarpur, Bihar, India Baba Ghulam Shah Badshah Univ, Sch Biosci & Biotechnol, Gene Express Lab, Rajouri, IndiaSarko, Diana K.论文数: 0 引用数: 0 h-index: 0机构: Southern Illinois Univ, Dept Anat, Sch Med, Carbondale, IL USA Baba Ghulam Shah Badshah Univ, Sch Biosci & Biotechnol, Gene Express Lab, Rajouri, IndiaRedwan, Elrashdy M.论文数: 0 引用数: 0 h-index: 0机构: King Abdulaziz Univ, Fac Sci, Biol Sci Dept, Jeddah, Saudi Arabia City Sci Res & Technol Applicat SRTA City, Genet Engn & Biotechnol Res Inst, Prot Res Dept, Alexandria, Egypt Baba Ghulam Shah Badshah Univ, Sch Biosci & Biotechnol, Gene Express Lab, Rajouri, India
- [4] Neural stem cells for disease modeling and evaluation of therapeutics for Tay-Sachs diseaseORPHANET JOURNAL OF RARE DISEASES, 2018, 13Vu, Mylinh论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USALi, Rong论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USABaskfield, Amanda论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USALu, Billy论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAFarkhondeh, Atena论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAGorshkov, Kirill论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAMotabar, Omid论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USABeers, Jeanette论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Ctr Mol Med, NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAChen, Guokai论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Ctr Mol Med, NIH, Bldg 10, Bethesda, MD 20892 USA Univ Macau, Fac Hlth Sci, Macau, Peoples R China NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAZou, Jizhong论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Ctr Mol Med, NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAEspejo-Mojica, Angela J.论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Javeriana, Fac Sci, Inst Study Inborn Errors Metab, Bogota, Colombia NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USARodriguez-Lopez, Alexander论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Javeriana, Fac Sci, Inst Study Inborn Errors Metab, Bogota, Colombia Pontificia Univ Javeriana, Fac Sci, Chem Dept, Bogota, Colombia NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAAlmeciga-Diaz, Carlos J.论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Javeriana, Fac Sci, Inst Study Inborn Errors Metab, Bogota, Colombia NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USABarrera, Luis A.论文数: 0 引用数: 0 h-index: 0机构: Pontificia Univ Javeriana, Fac Sci, Inst Study Inborn Errors Metab, Bogota, Colombia NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAJiang, Xuntian论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Diabet Cardiovasc Dis Ctr, St Louis, MO USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAOry, Daniel S.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Diabet Cardiovasc Dis Ctr, St Louis, MO USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAMarugan, Juan J.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USAZheng, Wei论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, Bldg 10, Bethesda, MD 20892 USA
- [5] Neural stem cells for disease modeling and evaluation of therapeutics for Tay-Sachs diseaseOrphanet Journal of Rare Diseases, 13Mylinh Vu论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesRong Li论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesAmanda Baskfield论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesBilly Lu论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesAtena Farkhondeh论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesKirill Gorshkov论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesOmid Motabar论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesJeanette Beers论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesGuokai Chen论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesJizhong Zou论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesAngela J. Espejo-Mojica论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesAlexander Rodríguez-López论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesCarlos J. Alméciga-Díaz论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesLuis A. Barrera论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesXuntian Jiang论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesDaniel S. Ory论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesJuan J. Marugan论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational SciencesWei Zheng论文数: 0 引用数: 0 h-index: 0机构: National Institutes of Health,National Center for Advancing Translational Sciences
- [6] Genome Editing in Stem Cells for Disease TherapeuticsMOLECULAR BIOTECHNOLOGY, 2018, 60 (04) : 329 - 338Song, Minjung论文数: 0 引用数: 0 h-index: 0机构: Silla Univ, Dept Food Biotechnol, Coll Med & Life Sci, Busan, South Korea Silla Univ, Dept Food Biotechnol, Coll Med & Life Sci, Busan, South KoreaRamakrishna, Suresh论文数: 0 引用数: 0 h-index: 0机构: Hanyang Univ, Grad Sch Biomed Sci & Engn, Seoul, South Korea Hanyang Univ, Coll Med, Seoul, South Korea Silla Univ, Dept Food Biotechnol, Coll Med & Life Sci, Busan, South Korea
- [7] Genome Editing in Stem Cells for Disease TherapeuticsMolecular Biotechnology, 2018, 60 : 329 - 338Minjung Song论文数: 0 引用数: 0 h-index: 0机构: Silla University,Department of Food Biotechnology, College of Medical and Life ScienceSuresh Ramakrishna论文数: 0 引用数: 0 h-index: 0机构: Silla University,Department of Food Biotechnology, College of Medical and Life Science
- [8] Editorial: Modeling Neurodegeneration in YeastFRONTIERS IN MOLECULAR NEUROSCIENCE, 2021, 14Braun, Ralf J.论文数: 0 引用数: 0 h-index: 0机构: Danube Private Univ, Res Div Neurodegenerat Dis, Ctr Biosci, Krems An Der Donau, Austria Danube Private Univ, Res Div Neurodegenerat Dis, Ctr Biosci, Krems An Der Donau, AustriaButtner, Sabrina论文数: 0 引用数: 0 h-index: 0机构: Stockholm Univ, Wenner Gren Inst, Dept Mol Biosci, Stockholm, Sweden Karl Franzens Univ Graz, Inst Mol Biosci, Graz, Austria Danube Private Univ, Res Div Neurodegenerat Dis, Ctr Biosci, Krems An Der Donau, Austria
- [9] Induced Pluripotent Stem Cells for Disease Modeling and Evaluation of Therapeutics for Niemann-Pick Disease Type ASTEM CELLS TRANSLATIONAL MEDICINE, 2016, 5 (12) : 1644 - 1655Long, Yan论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA Chinese Acad Sci, Guangzhou Inst Biomed & Hlth, Guangzhou, Guangdong, Peoples R China NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USAXu, Miao论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA Zhejiang Univ, Sch Med, Sir Run Run Shaw Hosp, Hangzhou, Zhejiang, Peoples R China NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USALi, Rong论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USADai, Sheng论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA Zhejiang Univ, Sch Med, Sir Run Run Shaw Hosp, Hangzhou, Zhejiang, Peoples R China NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USABeers, Jeanette论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Ctr Mol Med, NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USAChen, Guokai论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Ctr Mol Med, NIH, Bldg 10, Bethesda, MD 20892 USA Univ Macau, Fac Hlth Sci, Macau, Peoples R China NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USASoheilian, Ferri论文数: 0 引用数: 0 h-index: 0机构: Leidos Biomed Res Inc, Frederick Natl Lab Canc Res, Canc Res Technol Program, Electron Microscopy Lab, Frederick, MD USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USABaxa, Ulrich论文数: 0 引用数: 0 h-index: 0机构: Leidos Biomed Res Inc, Frederick Natl Lab Canc Res, Canc Res Technol Program, Electron Microscopy Lab, Frederick, MD USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USAWang, Mengqiao论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USAMarugan, Juan J.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USAMuro, Silvia论文数: 0 引用数: 0 h-index: 0机构: Univ Maryland, Inst Biosci & Biotechnol Res, College Pk, MD 20742 USA Univ Maryland, Fischell Dept Bioengn, College Pk, MD 20742 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USALi, Zhiyuan论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Guangzhou Inst Biomed & Hlth, Guangzhou, Guangdong, Peoples R China NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USABrady, Roscoe论文数: 0 引用数: 0 h-index: 0机构: NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USAZheng, Wei论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA NIH, Natl Ctr Advancing Translat Sci, 9800 Med Ctr Dr,MSC 3375, Bethesda, MD 20892 USA
- [10] iPS-derived neural stem cells for disease modeling and evaluation of therapeutics for mucopolysaccharidosis type IIEXPERIMENTAL CELL RESEARCH, 2022, 412 (01)Hong, Junjie论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Zhejiang Univ, Sir Run Run Shaw Hosp, Sch Med, Dept Gen Surg,Key Lab Laparoscop Technol Zhejiang, Hangzhou, Zhejiang, Peoples R China Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USACheng, Yu-Shan论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USAYang, Shu论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USASwaroop, Manju论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USAXu, Miao论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USABeers, Jeanette论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Heart,Lung & Blood Inst, iPSC Core Facil, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USAZou, Jizhong论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Heart,Lung & Blood Inst, iPSC Core Facil, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USAHuang, Wenwei论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USAMarugan, Juan J.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USACai, Xiujun论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Sir Run Run Shaw Hosp, Sch Med, Dept Gen Surg,Key Lab Laparoscop Technol Zhejiang, Hangzhou, Zhejiang, Peoples R China Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USAZheng, Wei论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA Natl Inst Hlth, Natl Ctr Adv Translat Sci, Bethesda, MD USA