Improved Survival with Asfotase Alfa Treatment in Pediatric Patients with Hypophosphatasia at High Risk of Death

被引:0
|
作者
Whyte, Michael [1 ]
Rockman-Greenberg, Cheryl [2 ]
Hofmann, Christine [3 ]
Leung, Edward C. W. [2 ]
Moseley, Scott [4 ]
Fujita, Kenji P. [4 ]
Melian, Agustin
Thompson, David
Liese, Johannes [3 ]
机构
[1] Shriners Hosp Children St Louis, St Louis, MO USA
[2] Univ Manitoba, Winnipeg, MB R3T 2N2, Canada
[3] Univ Wurzburg, Univ Childrens Hosp, Wurzburg, Germany
[4] Alex Pharmaceut, New York, NY USA
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R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
1097
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页码:S33 / S33
页数:1
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