Induction of Fetal Hemoglobin in Adult Erythroblasts by Genome Editing of the Beta-Globin Locus

被引：1
|
作者：
Antoniani, Chiara [1 ]
Lattanzi, Annalisa [2 ]
Pavani, Giulia [2 ]
Meneghini, Vasco [1 ]
Magrin, Elisa [1 ]
Weber, Leslie [1 ]
Porteus, Matthew [3 ]
Cavazzana, Marina [1 ]
Mavilio, Fulvio [2 ]
Miccio, Annarita [1 ]
机构：
[1] Imagine Inst, Paris, France
[2] Genethon, Evry, France
[3] Stanford Univ, Stanford, CA 94305 USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33367-6
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
559
引用
收藏
页码：S223 / S224
页数：2
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