A Randomized, Double-Blind, Placebo-Controlled, Gene-Delivery Clinical Trial of rAAVrh74.MHCK7.micro-dystrophin for Duchenne Muscular Dystrophy

被引：0
|
作者：
Mendell, Jerry R. [1 ,2 ]
Shieh, Perry B. [3 ]
Sahenk, Zarife [1 ]
Lehman, Kelly [1 ]
Lowes, Linda P. [1 ]
Reash, Natalie F. [1 ]
Iammarino, Megan [1 ]
Alfano, Lindsay N. [1 ]
Woods, Jeremy D. [3 ]
Skura, Christy L. [3 ]
Mao, Howard C. [3 ]
Staudt, Loretta A. [3 ]
Potter, Rachael A. [1 ,4 ]
Griffin, Danielle [1 ,4 ]
Lewis, Sarah [1 ,4 ]
Hu, Larry [4 ]
Upadhyay, Sameer [4 ]
Singh, Teji [4 ]
Rodino-Klapac, Louise R. [4 ]
机构：
[1] Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA
[2] Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA
[3] Ronald Reagan UCLA Med Ctr, Los Angeles, CA USA
[4] Sarepta Therapeut Inc, Cambridge, MA USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
231
引用
收藏
页码：120 / 121
页数：2
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